Prevalence, incidence and carrier frequency of 5q-linked spinal muscular atrophy - a literature review.
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Indirect estimation of the prevalence of spinal muscular atrophy Type I, II, and III in the United States.Motor Neuron Gene Therapy: Lessons from Spinal Muscular Atrophy for Amyotrophic Lateral Sclerosis.Overview of Current Drugs and Molecules in Development for Spinal Muscular Atrophy Therapy.Inflammation in CNS Neurodegenerative Diseases.An overview of the Cure SMA membership database: Highlights of key demographic and clinical characteristics of SMA members.Nusinersen for spinal muscular atrophy.Antisense oligonucleotides in neurological disorders.Position Statement: Sharing of Clinical Research Data in Spinal Muscular Atrophy to Accelerate Research and Improve Outcomes for Patients.Treatment Algorithm for Infants Diagnosed with Spinal Muscular Atrophy through Newborn Screening.UBA1/GARS-dependent pathways drive sensory-motor connectivity defects in spinal muscular atrophySpinal muscular atrophy within Amish and Mennonite populations: Ancestral haplotypes and natural history
P2860
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P2860
Prevalence, incidence and carrier frequency of 5q-linked spinal muscular atrophy - a literature review.
description
2017 nî lūn-bûn
@nan
2017 թուականի Յուլիսին հրատարակուած գիտական յօդուած
@hyw
2017 թվականի հուլիսին հրատարակված գիտական հոդված
@hy
2017年の論文
@ja
2017年論文
@yue
2017年論文
@zh-hant
2017年論文
@zh-hk
2017年論文
@zh-mo
2017年論文
@zh-tw
2017年论文
@wuu
name
Prevalence, incidence and carr ...... atrophy - a literature review.
@ast
Prevalence, incidence and carr ...... atrophy - a literature review.
@en
type
label
Prevalence, incidence and carr ...... atrophy - a literature review.
@ast
Prevalence, incidence and carr ...... atrophy - a literature review.
@en
prefLabel
Prevalence, incidence and carr ...... atrophy - a literature review.
@ast
Prevalence, incidence and carr ...... atrophy - a literature review.
@en
P2093
P2860
P50
P1476
Prevalence, incidence and carr ...... atrophy - a literature review
@en
P2093
Agata Robertson
Cynthia C Jones
Ian J Wilson
Shona Cameron
Suzanne F Cook
P2860
P2888
P356
10.1186/S13023-017-0671-8
P5008
P577
2017-07-04T00:00:00Z
P6179
1090386228