Genome editing with Cas9 in adult mice corrects a disease mutation and phenotype. - Wikidata - wikimedia - TriplyDB

Genome editing with Cas9 in adult mice corrects a disease mutation and phenotype.

Genome editing with Cas9 in adult mice corrects a disease mutation and phenotype.

http://www.wikidata.org/entity/Q34040385

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Biotechnology. A prudent path forward for genomic engineering and germline gene modification Multi-OMICs and Genome Editing Perspectives on Liver Cancer Signaling Networks A Broad Overview and Review of CRISPR-Cas Technology and Stem Cells Clinical development of gene therapy: results and lessons from recent successes Spermatogonial stem cell autotransplantation and germline genomic editing: a future cure for spermatogenic failure and prevention of transmission of genomic diseases In Vivo Delivery Systems for Therapeutic Genome Editing Genetic manipulation for inherited neurodegenerative diseases: myth or reality?The Rise of CRISPR/Cas for Genome Editing in Stem Cells The therapeutic potential of genome editing for β-thalassemia Genome-editing Technologies for Gene and Cell Therapy Making sense of GWAS: using epigenomics and genome engineering to understand the functional relevance of SNPs in non-coding regions of the human genome Genome Editing and Its Applications in Model Organisms Gene therapy: progress and predictions Towards a new era in medicine: therapeutic genome editing Beyond editing: repurposing CRISPR-Cas9 for precision genome regulation and interrogation Neuroprotective therapies in glaucoma: II. Genetic nanotechnology tools Minimizing off-Target Mutagenesis Risks Caused by Programmable Nucleases From Gene Targeting to Genome Editing: Transgenic animals applications and beyond Designed nucleases for targeted genome editing The CRISPR revolution and its impact on cancer research Breaking bad: The mutagenic effect of DNA repair Advances in CRISPR-Cas9 genome engineering: lessons learned from RNA interference Epigenome engineering in cancer: fairytale or a realistic path to the clinic?Progress and prospects of engineered sequence-specific DNA modulating technologies for the management of liver diseases RNA-guided CRISPR-Cas technologies for genome-scale investigation of disease processes CRISPR-Cas9 delivery to hard-to-transfect cells via membrane deformation Synthetic biology and occupational risk The potential for tumor suppressor gene therapy in head and neck cancer CRISPR-Cas9: from Genome Editing to Cancer Research Genome editing: the road of CRISPR/Cas9 from bench to clinic CRISPR-Cas: biology, mechanisms and relevance Using CRISPR/Cas to study gene function and model disease in vivo CRISPR/Cas9 and mitochondrial gene replacement therapy: promising techniques and ethical considerations CRISPR-Mediated Epigenome Editing The application of genome editing in studying hearing loss Knocking down disease: a progress report on siRNA therapeutics Progress with Recombinant Adeno-Associated Virus Vectors for Gene Therapy of Alpha-1 Antitrypsin Deficiency Liver-targeted gene therapy: Approaches and challenges Therapeutic genome editing: prospects and challenges Development and applications of CRISPR-Cas9 for genome engineering.

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Genome editing with Cas9 in adult mice corrects a disease mutation and phenotype.

http://www.wikidata.org/entity/Q34040385

description

2014 nî lūn-bûn

@nan

2014 թուականի Մարտին հրատարակուած գիտական յօդուած

@hyw

2014 թվականի մարտին հրատարակված գիտական հոդված

@hy

2014年の論文

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2014年論文

@yue

2014年論文

@zh-hant

2014年論文

@zh-hk

2014年論文

@zh-mo

2014年論文

@zh-tw

2014年论文

@wuu

name

Genome editing with Cas9 in adult mice corrects a disease mutation and phenotype.

@ast

Genome editing with Cas9 in adult mice corrects a disease mutation and phenotype.

@en

Genome editing with Cas9 in adult mice corrects a disease mutation and phenotype.

@nl

type

label

Genome editing with Cas9 in adult mice corrects a disease mutation and phenotype.

@ast

Genome editing with Cas9 in adult mice corrects a disease mutation and phenotype.

@en

Genome editing with Cas9 in adult mice corrects a disease mutation and phenotype.

@nl

prefLabel

Genome editing with Cas9 in adult mice corrects a disease mutation and phenotype.

@ast

Genome editing with Cas9 in adult mice corrects a disease mutation and phenotype.

@en

Genome editing with Cas9 in adult mice corrects a disease mutation and phenotype.

@nl

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P1433

Nature Biotechnology

P1476

Genome editing with Cas9 in adult mice corrects a disease mutation and phenotype

@en

P2093

Daniel G Anderson

http://www.w3.org/2001/XMLSchema#string

Eric Benedetti

http://www.w3.org/2001/XMLSchema#string

Hao Yin

http://www.w3.org/2001/XMLSchema#string

Phillip A Sharp

http://www.w3.org/2001/XMLSchema#string

Roman L Bogorad

http://www.w3.org/2001/XMLSchema#string

Sidi Chen

http://www.w3.org/2001/XMLSchema#string

Tyler Jacks

http://www.w3.org/2001/XMLSchema#string

P2860

RNA-guided human genome engineering via Cas9

Multiplex genome engineering using CRISPR/Cas systems

In vivo genome editing restores haemostasis in a mouse model of haemophilia

Targeted genome engineering in human cells with the Cas9 RNA-guided endonuclease

Functional repair of CFTR by CRISPR/Cas9 in intestinal stem cell organoids of cystic fibrosis patients

Point mutations in the murine fumarylacetoacetate hydrolase gene: Animal models for the human genetic disorder hereditary tyrosinemia type 1

Double nicking by RNA-guided CRISPR Cas9 for enhanced genome editing specificity

DNA targeting specificity of RNA-guided Cas9 nucleases

High-frequency off-target mutagenesis induced by CRISPR-Cas nucleases in human cells

SNP calling, genotype calling, and sample allele frequency estimation from New-Generation Sequencing data

P2888

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551-553

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scholarly article

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10.1038/NBT.2884

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6

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P478

32

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Victor Koteliansky

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2014-03-30T00:00:00Z

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261220435

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P698

24681508

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4157757

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