Early versus late treatment of spinal cord compression with long-term intrathecal enzyme replacement therapy in canine mucopolysaccharidosis type I.
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Pentosan Polysulfate: Oral Versus Subcutaneous Injection in Mucopolysaccharidosis Type I DogsIntra-articular enzyme replacement therapy with rhIDUA is safe, well-tolerated, and reduces articular GAG storage in the canine model of mucopolysaccharidosis type I.Diagnosis and treatment trends in mucopolysaccharidosis I: findings from the MPS I Registry.Systemic administration of tripeptidyl peptidase I in a mouse model of late infantile neuronal ceroid lipofuscinosis: effect of glycan modification.Effects of neonatal enzyme replacement therapy and simvastatin treatment on cervical spine disease in mucopolysaccharidosis I dogs.Arterial pathology in canine mucopolysaccharidosis-I and response to therapyBiodistribution and pharmacodynamics of recombinant human alpha-L-iduronidase (rhIDU) in mucopolysaccharidosis type I-affected cats following multiple intrathecal administrationsGlycosaminoglycan storage in neuroanatomical regions of mucopolysaccharidosis I dogs following intrathecal recombinant human iduronidase.Intrathecal gene therapy corrects CNS pathology in a feline model of mucopolysaccharidosis IIsokinetic muscle strength differences in patients with mucopolysaccharidosis I, II, and VIA review of gene therapy in canine and feline models of lysosomal storage disorders.Safety of laronidase delivered into the spinal canal for treatment of cervical stenosis in mucopolysaccharidosis I.Features of brain MRI in dogs with treated and untreated mucopolysaccharidosis type ILong-term nonsense suppression therapy moderates MPS I-H disease progression.Chronic Enzyme Replacement to the Brain of a Late Infantile Neuronal Ceroid Lipofuscinosis Mouse Has Differential Effects on Phenotypes of Disease.Nonsense Suppression as an Approach to Treat Lysosomal Storage Diseases.Orthopaedic aspects of mucopolysaccharidoses.Pathogenesis and treatment of spine disease in the mucopolysaccharidoses.Neonatal tolerance induction enables accurate evaluation of gene therapy for MPS I in a canine model.Postnatal progression of bone disease in the cervical spines of mucopolysaccharidosis I dogs.Widespread correction of central nervous system disease after intracranial gene therapy in a feline model of Sandhoff disease.Quantification of glycosaminoglycans in urine by isotope-dilution liquid chromatography-electrospray ionization tandem mass spectrometry.Disease stage determines the efficacy of treatment of a paediatric neurodegenerative disease.
P2860
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P2860
Early versus late treatment of spinal cord compression with long-term intrathecal enzyme replacement therapy in canine mucopolysaccharidosis type I.
description
2010 nî lūn-bûn
@nan
2010 թուականի Յուլիսին հրատարակուած գիտական յօդուած
@hyw
2010 թվականի հուլիսին հրատարակված գիտական հոդված
@hy
2010年の論文
@ja
2010年論文
@yue
2010年論文
@zh-hant
2010年論文
@zh-hk
2010年論文
@zh-mo
2010年論文
@zh-tw
2010年论文
@wuu
name
Early versus late treatment of ...... mucopolysaccharidosis type I.
@ast
Early versus late treatment of ...... mucopolysaccharidosis type I.
@en
Early versus late treatment of ...... mucopolysaccharidosis type I.
@nl
type
label
Early versus late treatment of ...... mucopolysaccharidosis type I.
@ast
Early versus late treatment of ...... mucopolysaccharidosis type I.
@en
Early versus late treatment of ...... mucopolysaccharidosis type I.
@nl
prefLabel
Early versus late treatment of ...... mucopolysaccharidosis type I.
@ast
Early versus late treatment of ...... mucopolysaccharidosis type I.
@en
Early versus late treatment of ...... mucopolysaccharidosis type I.
@nl
P2093
P2860
P1476
Early versus late treatment of ...... e mucopolysaccharidosis type I
@en
P2093
Agnes H Chen
Anton Mlikotic
Ashley Dierenfeld
Brigette L Tippin
Carole A Vogler
Catalina Guerra
Charles H Vite
Jackie Jens
Katherine P Ponder
Mark E Haskins
P2860
P304
P356
10.1016/J.YMGME.2010.06.020
P577
2010-07-23T00:00:00Z