Long-term enzymatic and phenotypic correction in the phenylketonuria mouse model by adeno-associated virus vector-mediated gene transfer.

Long-term enzymatic and phenotypic correction in the phenylketonuria mouse model by adeno-associated virus vector-mediated gene transfer.

Item
http://www.wikidata.org/entity/Q34325086
Complete correction of hyperphenylalaninemia following liver-directed, recombinant AAV2/8 vector-mediated gene therapy in murine phenylketonuria.AAV2/8-mediated correction of OTC deficiency is robust in adult but not neonatal Spf(ash) mice.Sexually dimorphic patterns of episomal rAAV genome persistence in the adult mouse liver and correlation with hepatocellular proliferationComparison of adeno-associated virus pseudotype 1, 2, and 8 vectors administered by intramuscular injection in the treatment of murine phenylketonuriaComplete and persistent phenotypic correction of phenylketonuria in mice by site-specific genome integration of murine phenylalanine hydroxylase cDNA.Phenylketonuria: an inborn error of phenylalanine metabolism.Treatment of phenylketonuria using minicircle-based naked-DNA gene transfer to murine liver.Protective effect of recombinant adeno-associated virus 2/8-mediated gene therapy from the maternal hyperphenylalaninemia in offsprings of a mouse model of phenylketonuria.Gene Therapy for the Treatment of Neurological Disorders: Metabolic Disorders.Potential of AAV vectors in the treatment of metabolic disease.Progress toward cell-directed therapy for phenylketonuria.Low therapeutic threshold for hepatocyte replacement in murine phenylketonuria.Correction of murine PKU following AAV-mediated intramuscular expression of a complete phenylalanine hydroxylating systemProtection of a ceramide synthase 2 null mouse from drug-induced liver injury: role of gap junction dysfunction and connexin 32 mislocalizationComplete restoration of phenylalanine oxidation in phenylketonuria mouse by a self-complementary adeno-associated virus vector.Administration-route and gender-independent long-term therapeutic correction of phenylketonuria (PKU) in a mouse model by recombinant adeno-associated virus 8 pseudotyped vector-mediated gene transfer.
P2860

Long-term enzymatic and phenotypic correction in the phenylketonuria mouse model by adeno-associated virus vector-mediated gene transfer.

Item
http://www.wikidata.org/entity/Q34325086
description
2004 nî lūn-bûn
@nan
2004 թուականի Յունիսին հրատարակուած գիտական յօդուած
@hyw
2004 թվականի հունիսին հրատարակված գիտական հոդված
@hy
2004年の論文
@ja
2004年論文
@yue
2004年論文
@zh-hant
2004年論文
@zh-hk
2004年論文
@zh-mo
2004年論文
@zh-tw
2004年论文
@wuu
name
Long-term enzymatic and phenot ...... vector-mediated gene transfer.
@ast
Long-term enzymatic and phenot ...... vector-mediated gene transfer.
@en
Long-term enzymatic and phenot ...... vector-mediated gene transfer.
@nl
type
label
Long-term enzymatic and phenot ...... vector-mediated gene transfer.
@ast
Long-term enzymatic and phenot ...... vector-mediated gene transfer.
@en
Long-term enzymatic and phenot ...... vector-mediated gene transfer.
@nl
prefLabel
Long-term enzymatic and phenot ...... vector-mediated gene transfer.
@ast
Long-term enzymatic and phenot ...... vector-mediated gene transfer.
@en
Long-term enzymatic and phenot ...... vector-mediated gene transfer.
@nl
P1433
P1476
P2093
P2860
P2888
P304
P31
P356
P407
P433
P478
P50
P577
P5875
P6179
P698
P921
P356
P1433
P1476
Long-term enzymatic and phenot ...... vector-mediated gene transfer.
@en
P2093
P2860
P2888
P304
P31
P356
10.1203/01.PDR.0000132837.29067.0E
P407
P433
P478
P50
P577
P5875
P6179
P698
P921