Prevention of muscular dystrophy in mice by CRISPR/Cas9-mediated editing of germline DNA
about
CRISPR/Cas9-mediated gene editing in human tripronuclear zygotesMulti-OMICs and Genome Editing Perspectives on Liver Cancer Signaling NetworksA Broad Overview and Review of CRISPR-Cas Technology and Stem CellsRecent advances in innovative therapeutic approaches for Duchenne muscular dystrophy: from discovery to clinical trialsSpermatogonial stem cell autotransplantation and germline genomic editing: a future cure for spermatogenic failure and prevention of transmission of genomic diseasesCustomizing the genome as therapy for the β-hemoglobinopathiesThe Rise of CRISPR/Cas for Genome Editing in Stem CellsGenome-editing Technologies for Gene and Cell TherapyMaking sense of GWAS: using epigenomics and genome engineering to understand the functional relevance of SNPs in non-coding regions of the human genomeGenome Editing and Its Applications in Model OrganismsMinimizing off-Target Mutagenesis Risks Caused by Programmable NucleasesFrom Gene Targeting to Genome Editing: Transgenic animals applications and beyondCRISPR/Cas9: a powerful genetic engineering tool for establishing large animal models of neurodegenerative diseasesPharmacology of manipulating lean body massThe CRISPR revolution and its impact on cancer researchAdvances in CRISPR-Cas9 genome engineering: lessons learned from RNA interferenceEpigenome engineering in cancer: fairytale or a realistic path to the clinic?RNA-guided CRISPR-Cas technologies for genome-scale investigation of disease processesEfficient Generation of Myostatin Knock-Out Sheep Using CRISPR/Cas9 Technology and Microinjection into ZygotesAnti-inflammatory drugs for Duchenne muscular dystrophy: focus on skeletal muscle-releasing factorsAdvances in gene therapy for muscular dystrophiesRecent Advances in the Molecular Genetics of Familial Hypertrophic Cardiomyopathy in South Asian DescendantsTranslation of Human-Induced Pluripotent Stem Cells: From Clinical Trial in a Dish to Precision MedicineThe application of genome editing in studying hearing lossAnimal models of Duchenne muscular dystrophy: from basic mechanisms to gene therapyThe CRISPR system can correct or modify the expression of genes responsible for hereditary diseasesTherapeutic genome editing: prospects and challengesA peptide encoded by a transcript annotated as long noncoding RNA enhances SERCA activity in muscleSevere myopathy in mice lacking the MEF2/SRF-dependent gene leiomodin-3Efficient Restoration of the Dystrophin Gene Reading Frame and Protein Structure in DMD Myoblasts Using the CinDel Method.CRISPR-mediated Genome Editing Restores Dystrophin Expression and Function in mdx MiceCRISPR-Cpf1 correction of muscular dystrophy mutations in human cardiomyocytes and mice.Animal models to improve our understanding and treatment of suicidal behaviorTherapeutic genome editing by combined viral and non-viral delivery of CRISPR system components in vivoLentiviral vectors can be used for full-length dystrophin gene therapyCRISPR/Cas9 Immune System as a Tool for Genome Engineering.Differentiation of spontaneously contracting cardiomyocytes from non-virally reprogrammed human amniotic fluid stem cells.CRISPR/Cas9-mediated genome editing via postnatal administration of AAV vector cures haemophilia B mice.Genome-wide association study identifies candidate genes for piglet splay leg syndrome in different populations.Spell Checking Nature: Versatility of CRISPR/Cas9 for Developing Treatments for Inherited Disorders.
P2860
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P2860
Prevention of muscular dystrophy in mice by CRISPR/Cas9-mediated editing of germline DNA
description
2014 nî lūn-bûn
@nan
2014 թուականի Օգոստոսին հրատարակուած գիտական յօդուած
@hyw
2014 թվականի օգոստոսին հրատարակված գիտական հոդված
@hy
2014年の論文
@ja
2014年論文
@yue
2014年論文
@zh-hant
2014年論文
@zh-hk
2014年論文
@zh-mo
2014年論文
@zh-tw
2014年论文
@wuu
name
Prevention of muscular dystrophy in mice by CRISPR/Cas9-mediated editing of germline DNA
@ast
Prevention of muscular dystrophy in mice by CRISPR/Cas9-mediated editing of germline DNA
@en
Prevention of muscular dystrophy in mice by CRISPR/Cas9-mediated editing of germline DNA
@nl
type
label
Prevention of muscular dystrophy in mice by CRISPR/Cas9-mediated editing of germline DNA
@ast
Prevention of muscular dystrophy in mice by CRISPR/Cas9-mediated editing of germline DNA
@en
Prevention of muscular dystrophy in mice by CRISPR/Cas9-mediated editing of germline DNA
@nl
prefLabel
Prevention of muscular dystrophy in mice by CRISPR/Cas9-mediated editing of germline DNA
@ast
Prevention of muscular dystrophy in mice by CRISPR/Cas9-mediated editing of germline DNA
@en
Prevention of muscular dystrophy in mice by CRISPR/Cas9-mediated editing of germline DNA
@nl
P2093
P2860
P356
P1433
P1476
Prevention of muscular dystrophy in mice by CRISPR/Cas9-mediated editing of germline DNA
@en
P2093
Alex A Mireault
Chengzu Long
Eric N Olson
John M Shelton
John R McAnally
Rhonda Bassel-Duby
P2860
P304
P356
10.1126/SCIENCE.1254445
P407
P577
2014-08-14T00:00:00Z