Vector platforms for gene therapy of inherited retinopathies.
about
Genetic manipulation for inherited neurodegenerative diseases: myth or reality?Multiple Independent Oscillatory Networks in the Degenerating RetinaGene therapy of inherited retinal degenerations: prospects and challengesIn Vivo Analysis of Disease-Associated Point Mutations Unveils Profound Differences in mRNA Splicing of Peripherin-2 in Rod and Cone PhotoreceptorsBiology and therapy of inherited retinal degenerative disease: insights from mouse modelsVitreal delivery of AAV vectored Cnga3 restores cone function in CNGA3-/-/Nrl-/- mice, an all-cone model of CNGA3 achromatopsiaNovel Therapies in Development for Diabetic Macular Edema.Intraocular pressure reduction and neuroprotection conferred by bone marrow-derived mesenchymal stem cells in an animal model of glaucoma.Improved dual AAV vectors with reduced expression of truncated proteins are safe and effective in the retina of a mouse model of Stargardt disease.Retinal Gene Therapy: Current Progress and Future Prospects.AAV-mediated transduction and targeting of retinal bipolar cells with improved mGluR6 promoters in rodents and primates.Heparan Sulfate Binding Promotes Accumulation of Intravitreally Delivered Adeno-associated Viral Vectors at the Retina for Enhanced Transduction but Weakly Influences Tropism.G-quartet oligonucleotide mediated delivery of proteins into photoreceptors and retinal pigment epithelium via intravitreal injection.Report on the National Eye Institute Audacious Goals Initiative: Replacement of Retinal Ganglion Cells from Endogenous Cell Sources.Efficacy and safety of voretigene neparvovec (AAV2-hRPE65v2) in patients with RPE65-mediated inherited retinal dystrophy: a randomised, controlled, open-label, phase 3 trial.Gene therapy for achromatopsia.Retinal Gene Therapy: Surgical Vector Delivery in the Translation to Clinical Trials.AAV Vectors for FRET-Based Analysis of Protein-Protein Interactions in Photoreceptor Outer Segments.Parkin overexpression protects retinal ganglion cells against glutamate excitotoxicity.Limbal Approach-Subretinal Injection of Viral Vectors for Gene Therapy in Mice Retinal Pigment Epithelium.Sensorimotor Cortex Injection of Adeno-Associated Viral Vector Mediates Knockout of PTEN in Neurons of the Brain and Spinal Cord of Mice.Gene Therapy and Stem Cell Transplantation in Retinal Disease: The New Frontier.Inhibition of TRB3 Protects Photoreceptors against Endoplasmic Reticulum Stress-Induced Apoptosis after Experimental Retinal Detachment.Dual AAV Vectors for Stargardt Disease.Phenotypic characterization of P23H and S334ter rhodopsin transgenic rat models of inherited retinal degeneration.Recent Advancements in Gene Therapy for Hereditary Retinal Dystrophies.Synthetic adeno-associated viral vector efficiently targets mouse and non-human primate retina in vivo.Retinal Cyclic Nucleotide-Gated Channels: From Pathophysiology to Therapy.Synapse maintenance and restoration in the retina by NGL2.
P2860
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P2860
Vector platforms for gene therapy of inherited retinopathies.
description
2014 nî lūn-bûn
@nan
2014 թուականի Օգոստոսին հրատարակուած գիտական յօդուած
@hyw
2014 թվականի օգոստոսին հրատարակված գիտական հոդված
@hy
2014年の論文
@ja
2014年論文
@yue
2014年論文
@zh-hant
2014年論文
@zh-hk
2014年論文
@zh-mo
2014年論文
@zh-tw
2014年论文
@wuu
name
Vector platforms for gene therapy of inherited retinopathies.
@ast
Vector platforms for gene therapy of inherited retinopathies.
@en
Vector platforms for gene therapy of inherited retinopathies.
@nl
type
label
Vector platforms for gene therapy of inherited retinopathies.
@ast
Vector platforms for gene therapy of inherited retinopathies.
@en
Vector platforms for gene therapy of inherited retinopathies.
@nl
prefLabel
Vector platforms for gene therapy of inherited retinopathies.
@ast
Vector platforms for gene therapy of inherited retinopathies.
@en
Vector platforms for gene therapy of inherited retinopathies.
@nl
P2860
P1476
Vector platforms for gene therapy of inherited retinopathies
@en
P2093
Agostina Puppo
P2860
P304
P356
10.1016/J.PRETEYERES.2014.08.001
P577
2014-08-12T00:00:00Z