piggyBac-mediated phenotypic correction of factor VIII deficiency
about
Shortened Lifespan and Lethal Hemorrhage in a Hemophilia A Mouse ModelOverexpression of factor VIII after AAV delivery is transiently associated with cellular stress in hemophilia A mice.Potential for cellular stress response to hepatic factor VIII expression from AAV vectorLong-term correction of hemophilia A mice following lentiviral mediated delivery of an optimized canine factor VIII gene.Preclinical and clinical advances in transposon-based gene therapy.
P2860
piggyBac-mediated phenotypic correction of factor VIII deficiency
description
2014 nî lūn-bûn
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2014 թուականի Սեպտեմբերին հրատարակուած գիտական յօդուած
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2014 թվականի սեպտեմբերին հրատարակված գիտական հոդված
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2014年の論文
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2014年学术文章
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2014年学术文章
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2014年学术文章
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2014年学术文章
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2014年学术文章
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2014年學術文章
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name
piggyBac-mediated phenotypic correction of factor VIII deficiency
@ast
piggyBac-mediated phenotypic correction of factor VIII deficiency
@en
type
label
piggyBac-mediated phenotypic correction of factor VIII deficiency
@ast
piggyBac-mediated phenotypic correction of factor VIII deficiency
@en
prefLabel
piggyBac-mediated phenotypic correction of factor VIII deficiency
@ast
piggyBac-mediated phenotypic correction of factor VIII deficiency
@en
P2860
P50
P356
P1476
piggyBac-mediated phenotypic correction of factor VIII deficiency
@en
P2093
Angela Arensdorf
Molly J Pollpeter
P2860
P356
10.1038/MTM.2014.42
P577
2014-09-10T00:00:00Z