Assessment of toxicity and biodistribution of recombinant AAV8 vector-mediated immunomodulatory gene therapy in mice with Pompe disease.

Assessment of toxicity and biodistribution of recombinant AAV8 vector-mediated immunomodulatory gene therapy in mice with Pompe disease.

Item
http://www.wikidata.org/entity/Q35184237
Targeted approaches to induce immune tolerance for Pompe disease therapyEnhanced efficacy from gene therapy in Pompe disease using coreceptor blockadePreclinical Development of New Therapy for Glycogen Storage Diseases.Synergistic Efficacy from Gene Therapy with Coreceptor Blockade and a β2-Agonist in Murine Pompe Disease.Safety and biodistribution assessment of sc-rAAV2.5IL-1Ra administered via intra-articular injection in a mono-iodoacetate-induced osteoarthritis rat modelLow-Dose Liver-Targeted Gene Therapy for Pompe Disease Enhances Therapeutic Efficacy of ERT via Immune Tolerance Induction.Dynamics of antigen presentation to transgene product-specific CD4+ T cells and of Treg induction upon hepatic AAV gene transfer.Long-term neurologic and cardiac correction by intrathecal gene therapy in Pompe disease.Double-target Antisense U1snRNAs Correct Mis-splicing Due to c.639+861C>T and c.639+919G>A GLA Deep Intronic Mutations.The Gene Therapy Resource Program: A Decade of Dedication to Translational Research by the National Heart, Lung, and Blood Institute.Immunomodulatory, liver depot gene therapy for Pompe disease.Combination Therapy Is the New Gene Therapy?
P2860

Assessment of toxicity and biodistribution of recombinant AAV8 vector-mediated immunomodulatory gene therapy in mice with Pompe disease.

Item
http://www.wikidata.org/entity/Q35184237
description
2014 nî lūn-bûn
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2014 թուականի Յունիսին հրատարակուած գիտական յօդուած
@hyw
2014 թվականի հունիսին հրատարակված գիտական հոդված
@hy
2014年の論文
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2014年学术文章
@wuu
2014年学术文章
@zh-cn
2014年学术文章
@zh-hans
2014年学术文章
@zh-my
2014年学术文章
@zh-sg
2014年學術文章
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name
Assessment of toxicity and bio ...... py in mice with Pompe disease.
@ast
Assessment of toxicity and bio ...... py in mice with Pompe disease.
@en
type
label
Assessment of toxicity and bio ...... py in mice with Pompe disease.
@ast
Assessment of toxicity and bio ...... py in mice with Pompe disease.
@en
prefLabel
Assessment of toxicity and bio ...... py in mice with Pompe disease.
@ast
Assessment of toxicity and bio ...... py in mice with Pompe disease.
@en
P1433
P1476
P2093
P2860
P304
P31
P356
P478
P577
P5875
P698
P921
P932
P356
P1433
P1476
Assessment of toxicity and bio ...... py in mice with Pompe disease.
@en
P2093
P2860
P304
P31
P356
P478
P577
P5875
P698
P921
P932