Vector design Tour de Force: integrating combinatorial and rational approaches to derive novel adeno-associated virus variants
about
Clinical development of gene therapy: results and lessons from recent successesTargeted approaches to induce immune tolerance for Pompe disease therapyHighly efficient baculovirus-mediated multigene delivery in primary cells.E Pluribus Unum: 50 Years of Research, Millions of Viruses, and One Goal--Tailored Acceleration of AAV EvolutionEvaluation of engineered AAV capsids for hepatic factor IX gene transfer in murine and canine modelsAn Immune-Competent Murine Model to Study Elimination of AAV-Transduced Hepatocytes by Capsid-Specific CD8+ T CellsCopackaged AAV9 Vectors Promote Simultaneous Immune Tolerance and Phenotypic Correction of Pompe Disease.Superior In vivo Transduction of Human Hepatocytes Using Engineered AAV3 Capsid.Application of polyploid adeno-associated virus vectors for transduction enhancement and neutralizing antibody evasion.Development of novel AAV serotype 6 based vectors with selective tropism for human cancer cells.Structure-guided evolution of antigenically distinct adeno-associated virus variants for immune evasion.Recent progress and considerations for AAV gene therapies targeting the central nervous system.Development of an inducible anti-VEGF rAAV gene therapy strategy for the treatment of wet AMD
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P2860
Vector design Tour de Force: integrating combinatorial and rational approaches to derive novel adeno-associated virus variants
description
2014 nî lūn-bûn
@nan
2014 թուականի Յուլիսին հրատարակուած գիտական յօդուած
@hyw
2014 թվականի հուլիսին հրատարակված գիտական հոդված
@hy
2014年の論文
@ja
2014年論文
@yue
2014年論文
@zh-hant
2014年論文
@zh-hk
2014年論文
@zh-mo
2014年論文
@zh-tw
2014年论文
@wuu
name
Vector design Tour de Force: i ...... deno-associated virus variants
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Vector design Tour de Force: i ...... deno-associated virus variants
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type
label
Vector design Tour de Force: i ...... deno-associated virus variants
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Vector design Tour de Force: i ...... deno-associated virus variants
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Vector design Tour de Force: i ...... deno-associated virus variants
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Vector design Tour de Force: i ...... deno-associated virus variants
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P2093
P2860
P356
P1433
P1476
Vector design Tour de Force: i ...... deno-associated virus variants
@en
P2093
Damien Marsic
David M Markusic
Lakshmanan Govindasamy
Roland W Herzog
Sergei Zolotukhin
Seth Currlin
Yu-Shan Tseng
P2860
P304
P356
10.1038/MT.2014.139
P577
2014-07-22T00:00:00Z