about
A plant-derived recombinant human glucocerebrosidase enzyme--a preclinical and phase I investigationBiodistribution and pharmacodynamics of recombinant human alpha-L-iduronidase (rhIDU) in mucopolysaccharidosis type I-affected cats following multiple intrathecal administrationsClinical manifestations and treatment of mucopolysaccharidosis type I patients in Latin America as compared with the rest of the world.The designer aminoglycoside NB84 significantly reduces glycosaminoglycan accumulation associated with MPS I-H in the Idua-W392X mouse.A novel, long-lived, and highly engraftable immunodeficient mouse model of mucopolysaccharidosis type I.A Dysmorphometric Analysis to Investigate Facial Phenotypic Signatures as a Foundation for Non-invasive Monitoring of Lysosomal Storage Disorders.Glycan-based biomarkers for mucopolysaccharidoses.Enzyme replacement therapy for Mucopolysaccharidosis Type I among patients followed within the MPS Brazil Network.Pre-transplant risk factors affecting outcome in Hurler syndrome.
P2860
Q21092136-824AA91E-131D-40AE-8D97-A37CC90EFFF0Q35088780-98B893A6-CE52-46A5-800D-10C1A661FDECQ35214507-A0B3F60A-4752-4BC2-B4C3-4538CCDC5C1AQ35661233-3934B0F7-2209-48D6-88CC-8484B0E5C088Q35665076-5201521D-4717-44F5-9A02-4ABC7742D204Q36590983-D3B0B815-2713-40B2-BE58-46CE59A02A86Q37161285-9ACFAF7B-1043-49B4-9DD3-EB5796B00ED6Q37644409-6401CFF7-4F34-490E-BD6D-A57D7E45D492Q51800411-112A6314-1454-4CF1-8CAD-91E9228AAED3
P2860
description
2005 nî lūn-bûn
@nan
2005年の論文
@ja
2005年論文
@yue
2005年論文
@zh-hant
2005年論文
@zh-hk
2005年論文
@zh-mo
2005年論文
@zh-tw
2005年论文
@wuu
2005年论文
@zh
2005年论文
@zh-cn
name
Laronidase treatment of mucopolysaccharidosis I.
@ast
Laronidase treatment of mucopolysaccharidosis I.
@en
type
label
Laronidase treatment of mucopolysaccharidosis I.
@ast
Laronidase treatment of mucopolysaccharidosis I.
@en
prefLabel
Laronidase treatment of mucopolysaccharidosis I.
@ast
Laronidase treatment of mucopolysaccharidosis I.
@en
P2093
P1433
P1476
Laronidase treatment of mucopolysaccharidosis I
@en
P2093
Ed J Wraith
John J Hopwood
Maria Fuller
P356
10.2165/00063030-200519010-00001
P577
2005-01-01T00:00:00Z
P6179
1027263498