Gene therapy progress and prospects: recent progress in transgene and RNAi expression cassettes.
about
Gene therapy for hemophiliaSelection of potent non-toxic inhibitory sequences from a randomized HIV-1 specific lentiviral short hairpin RNA library.Generation of cell lines to complement adenovirus vectors using recombination-mediated cassette exchange.RNA interference using a plasmid construct expressing short-hairpin RNAA novel gene therapy strategy using secreted multifunctional anti-HIV proteins to confer protection to gene-modified and unmodified target cells.An HDAC inhibitor enhances cancer therapeutic efficiency of RNA polymerase III promoter-driven IDO shRNA.A bidirectional promoter architecture enhances lentiviral transgenesis in embryonic and extraembryonic stem cells.The impact of intragenic CpG content on gene expression.Homogeneity and persistence of transgene expression by omitting antibiotic selection in cell line isolation.Systemic delivery of scAAV9 expressing SMN prolongs survival in a model of spinal muscular atrophy.Minimal doses of a sequence-optimized transgene mediate high-level and long-term EPO expression in vivo: challenging CpG-free gene design.A genetic strategy to treat sickle cell anemia by coregulating globin transgene expression and RNA interference.
P2860
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P2860
Gene therapy progress and prospects: recent progress in transgene and RNAi expression cassettes.
description
2005 nî lūn-bûn
@nan
2005年の論文
@ja
2005年論文
@yue
2005年論文
@zh-hant
2005年論文
@zh-hk
2005年論文
@zh-mo
2005年論文
@zh-tw
2005年论文
@wuu
2005年论文
@zh
2005年论文
@zh-cn
name
Gene therapy progress and pros ...... and RNAi expression cassettes.
@ast
Gene therapy progress and pros ...... and RNAi expression cassettes.
@en
type
label
Gene therapy progress and pros ...... and RNAi expression cassettes.
@ast
Gene therapy progress and pros ...... and RNAi expression cassettes.
@en
prefLabel
Gene therapy progress and pros ...... and RNAi expression cassettes.
@ast
Gene therapy progress and pros ...... and RNAi expression cassettes.
@en
P2860
P356
P1433
P1476
Gene therapy progress and pros ...... and RNAi expression cassettes.
@en
P2093
P2860
P2888
P304
P356
10.1038/SJ.GT.3302524
P577
2005-05-01T00:00:00Z