Genetic modification of hematopoietic stem cells with nonviral systems: past progress and future prospects.
about
Customizing the genome as therapy for the β-hemoglobinopathiesImproved delivery of Cas9 protein/gRNA complexes using lipofectamine CRISPRMAX.Long-term reproducible expression in human fetal liver hematopoietic stem cells with a UCOE-based lentiviral vectorErythroid-specific expression of β-globin from Sleeping Beauty-transduced human hematopoietic progenitor cells.Nanoparticles deliver triplex-forming PNAs for site-specific genomic recombination in CD34+ human hematopoietic progenitors.Nontoxic genetic engineering of mesenchymal stem cells using serum-compatible pullulan-spermine/DNA anioplexes.Biophysical effects in off-resonant gold nanoparticle mediated (GNOME) laser transfection of cell lines, primary- and stem cells using fs laser pulses.Characterization of nanoparticle mediated laser transfection by femtosecond laser pulses for applications in molecular medicine.Cationic liposome-mediated CXCR4 gene delivery into hematopoietic stem/progenitor cells: implications for clinical transplantation and gene therapy.Human erythropoietin gene delivery using an arginine-grafted bioreducible polymer system.A genome editing primer for the hematologistGene therapy for hemoglobinopathies: progress and challenges.Gene therapy for liver enzyme deficiencies: what have we learned from models for Crigler-Najjar and tyrosinemia?Site-specific Genome Editing in PBMCs With PLGA Nanoparticle-delivered PNAs Confers HIV-1 Resistance in Humanized Mice.Polymer delivery systems for site-specific genome editingRecent advances in targeted genome engineering in mammalian systems.Combining Single Strand Oligodeoxynucleotides and CRISPR/Cas9 to Correct Gene Mutations in β-Thalassemia-induced Pluripotent Stem Cells.RNA-based, transient modulation of gene expression in human haematopoietic stem and progenitor cells.Long-term and efficient expression of human β-globin gene in a hematopoietic cell line using a new site-specific integrating non-viral system.Efficient and rapid uptake of magnetic carbon nanotubes into human monocytic cells: implications for cell-based cancer gene therapy.Non-integrating lentiviral vectors based on the minimal S/MAR sequence retain transgene expression in dividing cells.Magnet-Bead Based MicroRNA Delivery System to Modify CD133+ Stem Cells.The β-globin Replicator greatly enhances the potential of S/MAR based episomal vectors for gene transfer into human haematopoietic progenitor cells.Gene Addition Strategies for β-Thalassemia and Sickle Cell Anemia.Gene therapy bio-safety: scientific and regulatory issues.Peptide Nucleic Acids as a Tool for Site-Specific Gene Editing.
P2860
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P2860
Genetic modification of hematopoietic stem cells with nonviral systems: past progress and future prospects.
description
2005 nî lūn-bûn
@nan
2005年の論文
@ja
2005年学术文章
@wuu
2005年学术文章
@zh-cn
2005年学术文章
@zh-hans
2005年学术文章
@zh-my
2005年学术文章
@zh-sg
2005年學術文章
@yue
2005年學術文章
@zh
2005年學術文章
@zh-hant
name
Genetic modification of hemato ...... progress and future prospects.
@ast
Genetic modification of hemato ...... progress and future prospects.
@en
type
label
Genetic modification of hemato ...... progress and future prospects.
@ast
Genetic modification of hemato ...... progress and future prospects.
@en
prefLabel
Genetic modification of hemato ...... progress and future prospects.
@ast
Genetic modification of hemato ...... progress and future prospects.
@en
P2093
P2860
P356
P1433
P1476
Genetic modification of hemato ...... progress and future prospects.
@en
P2093
Athanassiadou A
Papapetrou EP
Zoumbos NC
P2860
P2888
P304
P356
10.1038/SJ.GT.3302626
P478
12 Suppl 1
P577
2005-10-01T00:00:00Z