Intrathecal delivery of frataxin mRNA encapsulated in lipid nanoparticles to dorsal root ganglia as a potential therapeutic for Friedreich's ataxia.
about
Modified mRNA as a therapeutic tool to induce cardiac regeneration in ischemic heart disease.Pharmacological therapeutics in Friedreich ataxia: the present state.New Reasons to Pursue the Therapeutic Potential of Synthetic Nucleic Acids for Neurological Diseases.Sustained FXN expression in dorsal root ganglia from a nonreplicative genomic HSV-1 vector.Overexpression of Drosophila frataxin triggers cell death in an iron-dependent manner.A Novel Amino Lipid Series for mRNA Delivery: Improved Endosomal Escape and Sustained Pharmacology and Safety in Non-human Primates.Emerging therapeutics for the treatment of Friedreich’s ataxia
P2860
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P2860
Intrathecal delivery of frataxin mRNA encapsulated in lipid nanoparticles to dorsal root ganglia as a potential therapeutic for Friedreich's ataxia.
description
2016 nî lūn-bûn
@nan
2016年の論文
@ja
2016年論文
@yue
2016年論文
@zh-hant
2016年論文
@zh-hk
2016年論文
@zh-mo
2016年論文
@zh-tw
2016年论文
@wuu
2016年论文
@zh
2016年论文
@zh-cn
name
Intrathecal delivery of fratax ...... eutic for Friedreich's ataxia.
@ast
Intrathecal delivery of fratax ...... eutic for Friedreich's ataxia.
@en
type
label
Intrathecal delivery of fratax ...... eutic for Friedreich's ataxia.
@ast
Intrathecal delivery of fratax ...... eutic for Friedreich's ataxia.
@en
prefLabel
Intrathecal delivery of fratax ...... eutic for Friedreich's ataxia.
@ast
Intrathecal delivery of fratax ...... eutic for Friedreich's ataxia.
@en
P2093
P2860
P50
P356
P1433
P1476
Intrathecal delivery of fratax ...... eutic for Friedreich's ataxia.
@en
P2093
Braydon C Guild
Christine E Bulawa
Fazli Bozal
Kristy M Wood
Surya Bhamidipaty
Timothy P LaBranche
Varada P Rao
P2860
P2888
P356
10.1038/SREP20019
P407
P577
2016-02-17T00:00:00Z