Microdystrophin ameliorates muscular dystrophy in the canine model of duchenne muscular dystrophy
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Current and emerging treatment strategies for Duchenne muscular dystrophyThe emerging role of viral vectors as vehicles for DMD gene editingIntra-amniotic rAAV-mediated microdystrophin gene transfer improves canine X-linked muscular dystrophy and may induce immune toleranceAnimal models of Duchenne muscular dystrophy: from basic mechanisms to gene therapyPartial restoration of cardiac function with ΔPDZ nNOS in aged mdx model of Duchenne cardiomyopathy.Therapy of Genetic Disorders-Novel Therapies for Duchenne Muscular Dystrophy.The golden retriever model of Duchenne muscular dystrophy.The potential of adeno-associated viral vectors for gene delivery to muscle tissue.Progress and prospects of gene therapy clinical trials for the muscular dystrophies.Motor physical therapy affects muscle collagen type I and decreases gait speed in dystrophin-deficient dogs.AAV-8 is more efficient than AAV-9 in transducing neonatal dog heart.Duchenne muscular dystrophy gene therapy in the canine model.Porcine models of muscular dystrophySafe and bodywide muscle transduction in young adult Duchenne muscular dystrophy dogs with adeno-associated virus.Gene Therapy for Duchenne muscular dystrophy.Perspective on Adeno-Associated Virus Capsid Modification for Duchenne Muscular Dystrophy Gene TherapyExclusive skeletal muscle correction does not modulate dystrophic heart disease in the aged mdx model of Duchenne cardiomyopathyIn vivo genome editing improves muscle function in a mouse model of Duchenne muscular dystrophy.Prospect of gene therapy for cardiomyopathy in hereditary muscular dystrophy.Therapeutic advances in muscular dystrophyMicro-dystrophin and follistatin co-delivery restores muscle function in aged DMD model.Genomic removal of a therapeutic mini-dystrophin gene from adult mice elicits a Duchenne muscular dystrophy-like phenotypeThe Skeletal Muscle Environment and Its Role in Immunity and Tolerance to AAV Vector-Mediated Gene Transfer.Dual AAV gene therapy for Duchenne muscular dystrophy with a 7-kb mini-dystrophin gene in the canine model.Gene therapies that restore dystrophin expression for the treatment of Duchenne muscular dystrophy.Nanotherapy for Duchenne muscular dystrophy.Progress toward Gene Therapy for Duchenne Muscular Dystrophy.Long-term microdystrophin gene therapy is effective in a canine model of Duchenne muscular dystrophy.Antisense pre-treatment increases gene therapy efficacy in dystrophic muscles.A comparison of AAV strategies distinguishes overlapping vectors for efficient systemic delivery of the 6.2 kb Dysferlin coding sequenceA Five-Repeat Micro-Dystrophin Gene Ameliorated Dystrophic Phenotype in the Severe DBA/2J-mdx Model of Duchenne Muscular Dystrophy.The Gene Therapy Resource Program: A Decade of Dedication to Translational Research by the National Heart, Lung, and Blood Institute.Single-cut genome editing restores dystrophin expression in a new mouse model of muscular dystrophy.Inhibition of antigen presentation during AAV gene therapy using virus peptides.Micro-dystrophin gene therapy goes systemic in Duchenne muscular dystrophy patients.Treating pediatric neuromuscular disorders: The future is now.At the Crossroads of Clinical and Preclinical Research for Muscular Dystrophy-Are We Closer to Effective Treatment for Patients?Systemic AAV Micro-dystrophin Gene Therapy for Duchenne Muscular DystrophyGene and Cell Therapy for Muscular Dystrophies: Are We Getting There?
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Microdystrophin ameliorates muscular dystrophy in the canine model of duchenne muscular dystrophy
description
2013 nî lūn-bûn
@nan
2013年の論文
@ja
2013年論文
@yue
2013年論文
@zh-hant
2013年論文
@zh-hk
2013年論文
@zh-mo
2013年論文
@zh-tw
2013年论文
@wuu
2013年论文
@zh
2013年论文
@zh-cn
name
Microdystrophin ameliorates mu ...... of duchenne muscular dystrophy
@ast
Microdystrophin ameliorates mu ...... of duchenne muscular dystrophy
@en
type
label
Microdystrophin ameliorates mu ...... of duchenne muscular dystrophy
@ast
Microdystrophin ameliorates mu ...... of duchenne muscular dystrophy
@en
prefLabel
Microdystrophin ameliorates mu ...... of duchenne muscular dystrophy
@ast
Microdystrophin ameliorates mu ...... of duchenne muscular dystrophy
@en
P2093
P2860
P356
P1433
P1476
Microdystrophin ameliorates mu ...... of duchenne muscular dystrophy
@en
P2093
Chady H Hakim
Hsiao T Yang
Jin-Hong Shin
Keqing Zhang
Ronald L Terjung
Xiufang Pan
Yongping Yue
P2860
P304
P356
10.1038/MT.2012.283
P577
2013-01-15T00:00:00Z