Novel candidate disease for gene therapy: metachromatic leukodystrophy.

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Lentiviral vectors in gene therapy: their current status and future potential Four novel ARSA gene mutations with pathogenic impacts on metachromatic leukodystrophy: a bioinformatics approach to predict pathogenic mutations Development of gene therapy for thalassemia.

P2860

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P2860

Novel candidate disease for gene therapy: metachromatic leukodystrophy.

Item

http://www.wikidata.org/entity/Q36909371

description

2007 nî lūn-bûn

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2007年の論文

@ja

2007年論文

@yue

2007年論文

@zh-hant

2007年論文

@zh-hk

2007年論文

@zh-mo

2007年論文

@zh-tw

2007年论文

@wuu

2007年论文

@zh

2007年论文

@zh-cn

name

Novel candidate disease for gene therapy: metachromatic leukodystrophy.

@en

type

Item

label

Novel candidate disease for gene therapy: metachromatic leukodystrophy.

@en

prefLabel

Novel candidate disease for gene therapy: metachromatic leukodystrophy.

@en

P1476

Novel candidate disease for gene therapy: metachromatic leukodystrophy.

@en

P2093

Alessandra Biffi

http://www.w3.org/2001/XMLSchema#string

P2860

Sulfatases and sulfatase modifying factors: an exclusive and promiscuous relationship

SUMF1 enhances sulfatase activities in vivo in five sulfatase deficiencies

Viral vectors for gene therapy: the art of turning infectious agents into vehicles of therapeutics

Enzyme replacement improves nervous system pathology and function in a mouse model for metachromatic leukodystrophy

Hematopoietic stem cell gene transfer in a tumor-prone mouse model uncovers low genotoxicity of lentiviral vector integration

Transplantation of umbilical-cord blood in babies with infantile Krabbe's disease

Enzyme, cell and gene-based therapies for metachromatic leukodystrophy

Multiple sulfatase deficiency is caused by mutations in the gene encoding the human C(alpha)-formylglycine generating enzyme

The multiple sulfatase deficiency gene encodes an essential and limiting factor for the activity of sulfatases

In vivo gene delivery and stable transduction of nondividing cells by a lentiviral vector

P304

1193-1205

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scholarly article

P356

10.1517/14712598.7.8.1193

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English

P433

http://www.w3.org/2001/XMLSchema#string

P478

http://www.w3.org/2001/XMLSchema#string

P50

Luigi Naldini

P577

2007-08-01T00:00:00Z

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P698

17696818

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P921

gene therapy

Novel candidate disease for gene therapy: metachromatic leukodystrophy.

about

P2860

P2860

Novel candidate disease for gene therapy: metachromatic leukodystrophy.

description

name

type

label

prefLabel

P1433

P1476

P2093

P2860

P304

P31

P356

P407

P433

P478

P50

P577

P698

P921

P356

P1433

P1476

P2093

P2860

P304

P31

P356

P407

P433

P478

P50

P577

P698

P921