Widespread Central Nervous System Gene Transfer and Silencing After Systemic Delivery of Novel AAV-AS Vector.
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Adeno Associated Viral Vector Delivered RNAi for Gene Therapy of SOD1 Amyotrophic Lateral SclerosisIn Vivo Selection Yields AAV-B1 Capsid for Central Nervous System and Muscle Gene TherapyBetter Targeting, Better Efficiency for Wide-Scale Neuronal Transduction with the Synapsin Promoter and AAV-PHP.B.Tailored transgene expression to specific cell types in the central nervous system after peripheral injection with AAV9.Site-Specific PEGylated Adeno-Associated Viruses with Increased Serum Stability and Reduced Immunogenicity.Viral vectors for therapy of neurologic diseases.Future of rAAV Gene Therapy: Platform for RNAi, Gene Editing, and Beyond.Adeno-Associated Virus-Based Gene Therapy for CNS Diseases.Systemic delivery of adeno-associated viral vectors.Therapeutic Potential of Secreted Amyloid Precursor Protein APPsα.Engineered AAVs for efficient noninvasive gene delivery to the central and peripheral nervous systems.Brain endothelial cell-targeted gene therapy of neurovascular disorders.In vivo genome editing in animals using AAV-CRISPR system: applications to translational research of human disease.Engineered viral vectors for functional interrogation, deconvolution, and manipulation of neural circuits.Nuclease-Mediated Gene Therapies for Inherited Metabolic Diseases of the Liver.In vivo methods for acute modulation of gene expression in the central nervous systemNeuro-Immuno-Gene- and Genome-Editing-Therapy for Alzheimer's Disease: Are We There Yet?Systemic Delivery of MicroRNA Using Recombinant Adeno-associated Virus Serotype 9 to Treat Neuromuscular Diseases in Rodents
P2860
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P2860
Widespread Central Nervous System Gene Transfer and Silencing After Systemic Delivery of Novel AAV-AS Vector.
description
2015 nî lūn-bûn
@nan
2015年の論文
@ja
2015年論文
@yue
2015年論文
@zh-hant
2015年論文
@zh-hk
2015年論文
@zh-mo
2015年論文
@zh-tw
2015年论文
@wuu
2015年论文
@zh
2015年论文
@zh-cn
name
Widespread Central Nervous Sys ...... livery of Novel AAV-AS Vector.
@en
type
label
Widespread Central Nervous Sys ...... livery of Novel AAV-AS Vector.
@en
prefLabel
Widespread Central Nervous Sys ...... livery of Novel AAV-AS Vector.
@en
P2093
P2860
P356
P1433
P1476
Widespread Central Nervous Sys ...... livery of Novel AAV-AS Vector.
@en
P2093
Aime K Johnson
Allison M Keeler
Anne F Harris
Douglas R Martin
Ellen Sapp
Guangping Gao
Heather L Gray-Edwards
Jacob A Johnson
Jennifer S Ferreira
Lorelei Stoica
P2860
P304
P356
10.1038/MT.2015.231
P577
2015-12-28T00:00:00Z