Reprogramming metabolic pathways in vivo with CRISPR/Cas9 genome editing to treat hereditary tyrosinaemia
about
Genome editing for inborn errors of metabolism: advancing towards the clinic.CRISPR Editing in Biological and Biomedical Investigation.CRISPR/Cas9 system: a powerful technology for in vivo and ex vivo gene therapy.The CRISPR/Cas9 system: Their delivery, in vivo and ex vivo applications and clinical development by startups.CRISPR/Cas9: at the cutting edge of hepatology.Somatic genome editing with CRISPR/Cas9 generates and corrects a metabolic disease.Immunity to CRISPR Cas9 and Cas12a therapeutics.In vivo genome editing thrives with diversified CRISPR technologies.CRISPR Correction of a Homozygous Low-Density Lipoprotein Receptor Mutation in Familial Hypercholesterolemia Induced Pluripotent Stem Cells.Nuclease-Mediated Gene Therapies for Inherited Metabolic Diseases of the Liver.Exosome-Liposome Hybrid Nanoparticles Deliver CRISPR/Cas9 System in MSCs.All-in-one adeno-associated virus delivery and genome editing by Neisseria meningitidis Cas9 in vivoIn Vivo Genome Editing as a Therapeutic Approach
P2860
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P2860
Reprogramming metabolic pathways in vivo with CRISPR/Cas9 genome editing to treat hereditary tyrosinaemia
description
2016 թվականի օգոստոսի 30-ին հրատարակված գիտական հոդված
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article científic
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article scientifique
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articolo scientifico
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artigo científico
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bilimsel makale
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scientific article published on 30 August 2016
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vedecký článok
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vetenskaplig artikel
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videnskabelig artikel
@da
name
Reprogramming metabolic pathwa ...... treat hereditary tyrosinaemia
@en
Reprogramming metabolic pathwa ...... treat hereditary tyrosinaemia.
@nl
type
label
Reprogramming metabolic pathwa ...... treat hereditary tyrosinaemia
@en
Reprogramming metabolic pathwa ...... treat hereditary tyrosinaemia.
@nl
prefLabel
Reprogramming metabolic pathwa ...... treat hereditary tyrosinaemia
@en
Reprogramming metabolic pathwa ...... treat hereditary tyrosinaemia.
@nl
P2093
P2860
P356
P1476
Reprogramming metabolic pathwa ...... treat hereditary tyrosinaemia
@en
P2093
Beatrice Bissig-Choisat
Diane Yang
Francis P Pankowicz
Karl-Dimiter Bissig
Leroy Hubert
Malgorzata Borowiak
Mercedes Barzi
Milan Ravishankar
Pavel Sumazin
P2860
P2888
P356
10.1038/NCOMMS12642
P407
P577
2016-08-30T00:00:00Z