Antisense Oligonucleotides Used to Target the DUX4 mRNA as Therapeutic Approaches in FaciosScapuloHumeral Muscular Dystrophy (FSHD).
about
Nanopore-based single molecule sequencing of the D4Z4 array responsible for facioscapulohumeral muscular dystrophy.Overexpression of the double homeodomain protein DUX4c interferes with myofibrillogenesis and induces clustering of myonuclei.A cre-inducible DUX4 transgenic mouse model for investigating facioscapulohumeral muscular dystrophy.Facioscapulohumeral dystrophy: Activating an early embryonic transcriptional program in human skeletal muscle.Functional domains of the FSHD-associated DUX4 protein.
P2860
Antisense Oligonucleotides Used to Target the DUX4 mRNA as Therapeutic Approaches in FaciosScapuloHumeral Muscular Dystrophy (FSHD).
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article científic
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article scientifique
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articolo scientifico
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artigo científico
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bilimsel makale
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scientific article published on 03 March 2017
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vedecký článok
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vetenskaplig artikel
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videnskabelig artikel
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vědecký článek
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name
Antisense Oligonucleotides Use ...... ral Muscular Dystrophy (FSHD).
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Antisense Oligonucleotides Use ...... puloHumeral Muscular Dystrophy
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type
label
Antisense Oligonucleotides Use ...... ral Muscular Dystrophy (FSHD).
@en
Antisense Oligonucleotides Use ...... puloHumeral Muscular Dystrophy
@nl
prefLabel
Antisense Oligonucleotides Use ...... ral Muscular Dystrophy (FSHD).
@en
Antisense Oligonucleotides Use ...... puloHumeral Muscular Dystrophy
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P2093
P2860
P356
P1433
P1476
Antisense Oligonucleotides Use ...... ral Muscular Dystrophy (FSHD).
@en
P2093
Armelle Wauters
Céline Vanderplanck
Eugénie Ansseau
Frédérique Coppée
Scott Q Harper
P2860
P356
10.3390/GENES8030093
P577
2017-03-03T00:00:00Z