Current progress on gene therapy for primary immunodeficiencies.
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The interplay of post-translational modification and gene therapyCell-based therapy technology classifications and translational challengesGene therapy on the moveLentiviral vector transduction of spermatozoa as a tool for the study of early development.State-of-the-art human gene therapy: part II. Gene therapy strategies and clinical applications.Intravenous administration of retroviral replicating vector, Toca 511, demonstrates therapeutic efficacy in orthotopic immune-competent mouse glioma modelClinical applications of gene therapy for primary immunodeficiencies.Synthesis of bifunctional molecules containing [12]aneN3 and coumarin moieties as effective DNA condensation agents and new non-viral gene vectors.Lentiviral Vector-Mediated Correction of a Mouse Model of Leukocyte Adhesion Deficiency Type I.Efficiency and safety of O⁶-methylguanine DNA methyltransferase (MGMT(P140K))-mediated in vivo selection in a humanized mouse modelPreparation for a first-in-man lentivirus trial in patients with cystic fibrosis.The case for mandatory newborn screening for severe combined immunodeficiency (SCID).The renal Fanconi syndrome in cystinosis: pathogenic insights and therapeutic perspectives.
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Current progress on gene therapy for primary immunodeficiencies.
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article científic
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article scientifique
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articol științific
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articolo scientifico
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artigo científico
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artigo científico
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artigo científico
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artikel ilmiah
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artikull shkencor
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artículo científico
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Current progress on gene therapy for primary immunodeficiencies.
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Current progress on gene therapy for primary immunodeficiencies.
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Current progress on gene therapy for primary immunodeficiencies.
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P2093
P2860
P356
P1433
P1476
Current progress on gene therapy for primary immunodeficiencies.
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P2093
P2860
P2888
P304
P356
10.1038/GT.2013.21
P577
2013-05-30T00:00:00Z