Socio-economic burden of rare diseases: A systematic review of cost of illness evidence.
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Access to Orphan Drugs: A Comprehensive Review of Legislations, Regulations and Policies in 35 CountriesThe Genetic Basis of Mendelian Phenotypes: Discoveries, Challenges, and OpportunitiesThe burden, epidemiology, costs and treatment for Duchenne muscular dystrophy: an evidence reviewCystic fibrosis on the African continent.Health Economic Data in Reimbursement of New Medical Technologies: Importance of the Socio-Economic Burden as a Decision-Making CriterionA window into living with an undiagnosed disease: illness narratives from the Undiagnosed Diseases NetworkGene therapy for monogenic liver diseases: clinical successes, current challenges and future prospects.Social and economic costs and health-related quality of life in non-institutionalised patients with cystic fibrosis in the United Kingdom.Socioeconomic costs and health-related quality of life in juvenile idiopathic arthritis: a cost-of-illness study in the United Kingdom.Social/economic costs and health-related quality of life in patients with epidermolysis bullosa in EuropeEthical imperatives of timely access to orphan drugs: is possible to reconcile economic incentives and patients' health needs?Review of 11 national policies for rare diseases in the context of key patient needs.A Systematic Review of Cost-of-Illness Studies of Multimorbidity.Estimating Direct Cost of Cystic Fibrosis Care Using Irish Registry Healthcare Resource Utilisation Data, 2008-2012.Perceived economic burden associated with an inherited cardiac condition: a qualitative inquiry with families affected by arrhythmogenic right ventricular cardiomyopathy.Opportunities and technical challenges in next-generation sequencing for diagnosis of rare pediatric diseases.Economic burden and health-related quality of life associated with Prader-Willi syndrome in France.Social/economic costs and health-related quality of life in patients with juvenile idiopathic arthritis in Europe.Social/economic costs and health-related quality of life in patients with Prader-Willi syndrome in Europe.Social/economic costs and health-related quality of life in patients with scleroderma in Europe.Discovery of new diketopiperazines inhibiting Burkholderia cenocepacia quorum sensing in vitro and in vivoRare Diseases of the Anterior Segment of the Eye: Update on Diagnosis and ManagementThe health and life path of rare disease patients: results of the 2015 French barometer.Cost-of-Illness in Rare Diseases.Psychosocial Profiles of Parents of Children with Undiagnosed Diseases: Managing Well or Just Managing?Social/economic costs and health-related quality of life of mucopolysaccharidosis patients and their caregivers in Europe.Using multi-criteria decision analysis to appraise orphan drugs: a systematic review.Burden of disease scoring in epidermolysis bullosa.In silico clinical trials for pediatric orphan diseases.Patient reported outcome measures in rare diseases: a narrative review.Epidemiology of Sanfilippo syndrome: results of a systematic literature review.Characteristics of undiagnosed diseases network applicants: implications for referring providersMulti-Criteria Decision Analysis (MCDA) Models in Health Technology Assessment of Orphan Drugs-a Systematic Literature Review. Next Steps in Methodology Development?
P2860
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P2860
Socio-economic burden of rare diseases: A systematic review of cost of illness evidence.
description
2014 nî lūn-bûn
@nan
2014年の論文
@ja
2014年論文
@yue
2014年論文
@zh-hant
2014年論文
@zh-hk
2014年論文
@zh-mo
2014年論文
@zh-tw
2014年论文
@wuu
2014年论文
@zh
2014年论文
@zh-cn
name
Socio-economic burden of rare diseases: A systematic review of cost of illness evidence.
@en
type
label
Socio-economic burden of rare diseases: A systematic review of cost of illness evidence.
@en
prefLabel
Socio-economic burden of rare diseases: A systematic review of cost of illness evidence.
@en
P1433
P1476
Socio-economic burden of rare diseases: A systematic review of cost of illness evidence.
@en
P2093
Panos Kanavos
P304
P356
10.1016/J.HEALTHPOL.2014.12.016
P577
2014-12-30T00:00:00Z