The emperor's new dystrophin: finding sense in the noise.
about
Recent advances in innovative therapeutic approaches for Duchenne muscular dystrophy: from discovery to clinical trialsAssessment and management of respiratory function in patients with Duchenne muscular dystrophy: current and emerging optionsDystrophin and the two related genetic diseases, Duchenne and Becker muscular dystrophiesDystrophic Cardiomyopathy-Potential Role of Calcium in Pathogenesis, Treatment and Novel TherapiesImproving clinical trial design for Duchenne muscular dystrophy.Deletion of Dystrophin In-Frame Exon 5 Leads to a Severe Phenotype: Guidance for Exon Skipping Strategies.Digital Droplet PCR for the Absolute Quantification of Exon Skipping Induced by Antisense Oligonucleotides in (Pre-)Clinical Development for Duchenne Muscular Dystrophy.Translational development of splice-modifying antisense oligomers.Dystrophin and Spectrin, Two Highly Dissimilar Sisters of the Same Family.2'-O-Methyl RNA/Ethylene-Bridged Nucleic Acid Chimera Antisense Oligonucleotides to Induce Dystrophin Exon 45 Skipping.Synthesis of a Morpholino Nucleic Acid (MNA)-Uridine Phosphoramidite, and Exon Skipping Using MNA/2'-O-Methyl Mixmer Antisense Oligonucleotide.Normal and altered pre-mRNA processing in the DMD gene.Correction of the Exon 2 Duplication in DMD Myoblasts by a Single CRISPR/Cas9 System.Circulating miRNAs are generic and versatile therapeutic monitoring biomarkers in muscular dystrophies.Rational Design of Short Locked Nucleic Acid-Modified 2′-O-Methyl Antisense Oligonucleotides for Efficient Exon-Skipping In Vitro.Dystrophin's central domain forms a complex filament that becomes disorganized by in-frame deletions.Treating pediatric neuromuscular disorders: The future is now.RNA Editing for Muscular Dystrophy Therapy
P2860
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P2860
The emperor's new dystrophin: finding sense in the noise.
description
2015 nî lūn-bûn
@nan
2015年の論文
@ja
2015年論文
@yue
2015年論文
@zh-hant
2015年論文
@zh-hk
2015年論文
@zh-mo
2015年論文
@zh-tw
2015年论文
@wuu
2015年论文
@zh
2015年论文
@zh-cn
name
The emperor's new dystrophin: finding sense in the noise.
@en
type
label
The emperor's new dystrophin: finding sense in the noise.
@en
prefLabel
The emperor's new dystrophin: finding sense in the noise.
@en
P1476
The emperor's new dystrophin: finding sense in the noise.
@en
P2093
P304
P356
10.1016/J.MOLMED.2015.04.006
P50
P577
2015-06-04T00:00:00Z