Selection-free gene repair after adenoviral vector transduction of designer nucleases: rescue of dystrophin synthesis in DMD muscle cell populations.
about
Current and emerging treatment strategies for Duchenne muscular dystrophyThe emerging role of viral vectors as vehicles for DMD gene editingAdvances in gene therapy for muscular dystrophiesAdenoviral vectors encoding CRISPR/Cas9 multiplexes rescue dystrophin synthesis in unselected populations of DMD muscle cells.The CRB1 Complex: Following the Trail of Crumbs to a Feasible Gene Therapy Strategy.Exon skipping: a first in class strategy for Duchenne muscular dystrophy.CRISPR: express delivery to any DNA address.A comprehensive overview of computational resources to aid in precision genome editing with engineered nucleases.CRISPR/Cas9 Flexes Its Muscles: In Vivo Somatic Gene Editing for Muscular DystrophyGenome Editing of Monogenic Neuromuscular Diseases: A Systematic Review.Therapeutic gene editing: delivery and regulatory perspectivesNanotherapy for Duchenne muscular dystrophy.Cellular Reprogramming, Genome Editing, and Alternative CRISPR Cas9 Technologies for Precise Gene Therapy of Duchenne Muscular Dystrophy.Probing the impact of chromatin conformation on genome editing tools.Genome engineering: a new approach to gene therapy for neuromuscular disorders.CRISPR/Cas9-Mediated Deletion of CTG Expansions Recovers Normal Phenotype in Myogenic Cells Derived from Myotonic Dystrophy 1 Patients.Correction of diverse muscular dystrophy mutations in human engineered heart muscle by single-site genome editing.A New Kid on the Playground of CRISPR DMD Therapy.Delivering CRISPR: a review of the challenges and approaches
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P2860
Selection-free gene repair after adenoviral vector transduction of designer nucleases: rescue of dystrophin synthesis in DMD muscle cell populations.
description
2016 nî lūn-bûn
@nan
2016年の論文
@ja
2016年論文
@yue
2016年論文
@zh-hant
2016年論文
@zh-hk
2016年論文
@zh-mo
2016年論文
@zh-tw
2016年论文
@wuu
2016年论文
@zh
2016年论文
@zh-cn
name
Selection-free gene repair aft ...... n DMD muscle cell populations.
@en
type
label
Selection-free gene repair aft ...... n DMD muscle cell populations.
@en
prefLabel
Selection-free gene repair aft ...... n DMD muscle cell populations.
@en
P2860
P50
P356
P1476
Selection-free gene repair aft ...... in DMD muscle cell populations
@en
P2093
Ignazio Maggio
P2860
P304
P356
10.1093/NAR/GKV1540
P407
P577
2016-01-13T00:00:00Z