Liver gene therapy by lentiviral vectors reverses anti-factor IX pre-existing immunity in haemophilic mice
about
Role of the vector genome and underlying factor IX mutation in immune responses to AAV gene therapy for hemophilia BGene therapy for hemophiliaGene therapy in an era of emerging treatment options for hemophilia BStem cell transplantation for muscular dystrophy: the challenge of immune response.Cell-Mediated Immunity to AAV Vectors, Evolving Concepts and Potential Solutions.Development of Gene Transfer for Induction of Antigen-specific Tolerance.Prevalence of anti-adeno-associated virus serotype 8 neutralizing antibodies and arylsulfatase B cross-reactive immunologic material in mucopolysaccharidosis VI patient candidates for a gene therapy trial.Effects of FVIII immunity on hepatocyte and hematopoietic stem cell-directed gene therapy of murine hemophilia A.Pre-existing Antibody: Biotherapeutic Modality-Based Review.Induction of Hematopoietic Microchimerism by Gene-Modified BMT Elicits Antigen-Specific B and T Cell Unresponsiveness toward Gene Therapy ProductsEffective gene therapy for haemophilic mice with pathogenic factor IX antibodies.Low-dose Gene Therapy Reduces the Frequency of Enzyme Replacement Therapy in a Mouse Model of Lysosomal Storage Disease.Low-Dose Liver-Targeted Gene Therapy for Pompe Disease Enhances Therapeutic Efficacy of ERT via Immune Tolerance Induction.New approaches to gene and cell therapy for hemophilia.In vivo induction of regulatory T cells for immune tolerance in hemophilia.Gene therapy for immune tolerance induction in hemophilia with inhibitors.Murine Rankl-/- Mesenchymal Stromal Cells Display an Osteogenic Differentiation Defect Improved by a RANKL-Expressing Lentiviral Vector.Complexity of immune responses to AAV transgene products - Example of factor IX.Dynamics of antigen presentation to transgene product-specific CD4+ T cells and of Treg induction upon hepatic AAV gene transfer.Insulin B chain 9-23 gene transfer to hepatocytes protects from type 1 diabetes by inducing Ag-specific FoxP3+ Tregs.Liver-directed lentiviral gene therapy in a dog model of hemophilia B.A Novel Platform for Immune Tolerance Induction in Hemophilia A Mice.In vivo knockdown of antisense non-coding mitochondrial RNAs by a lentiviral-encoded shRNA inhibits melanoma tumor growth and lung colonization.Gene Therapy With Regulatory T Cells: A Beneficial Alliance.Lessons learned from lung and liver in-vivo gene therapy: implications for the future
P2860
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P2860
Liver gene therapy by lentiviral vectors reverses anti-factor IX pre-existing immunity in haemophilic mice
description
2013 nî lūn-bûn
@nan
2013年の論文
@ja
2013年論文
@yue
2013年論文
@zh-hant
2013年論文
@zh-hk
2013年論文
@zh-mo
2013年論文
@zh-tw
2013年论文
@wuu
2013年论文
@zh
2013年论文
@zh-cn
name
Liver gene therapy by lentivir ...... g immunity in haemophilic mice
@en
Liver gene therapy by lentivir ...... immunity in haemophilic mice.
@nl
type
label
Liver gene therapy by lentivir ...... g immunity in haemophilic mice
@en
Liver gene therapy by lentivir ...... immunity in haemophilic mice.
@nl
prefLabel
Liver gene therapy by lentivir ...... g immunity in haemophilic mice
@en
Liver gene therapy by lentivir ...... immunity in haemophilic mice.
@nl
P2093
P2860
P50
P921
P356
P1476
Liver gene therapy by lentivir ...... g immunity in haemophilic mice
@en
P2093
Fabio Russo
Kevin Goudy
Sara Bartolaccini
P2860
P304
P356
10.1002/EMMM.201302857
P50
P577
2013-09-16T00:00:00Z