about
Developing multidisciplinary clinics for neuromuscular care and research.miRNA in spinal muscular atrophy pathogenesis and therapy.Contrast-Enhanced Near-Infrared Optical Imaging Detects Exacerbation and Amelioration of Murine Muscular Dystrophy.Nusinersen: The First Option Beyond Supportive Care for Spinal Muscular Atrophy.Overview of Current Drugs and Molecules in Development for Spinal Muscular Atrophy Therapy.Justifiability and Animal Research in Health: Can Democratisation Help Resolve Difficulties?Computational identification and validation of alternative splicing in ZSF1 rat RNA-seq data, a preclinical model for type 2 diabetic nephropathy.Autism spectrum disorder: prospects for treatment using gene therapy.Engineering Nanoparticles for Targeted Delivery of Nucleic Acid Therapeutics in Tumor
P2860
Q39386238-FC4FBD3B-816B-41D5-AEDC-8742393D14A8Q47379842-6BA319D6-0469-4F49-A511-25FF5D9BA7F1Q47561363-6A2F1805-7D32-41AE-9CA5-735868CA8F61Q48014486-2B9F79C3-1B2D-4C15-A9B8-D38B4382FBA0Q48144714-308DDA00-BFE8-40ED-96BD-D7933FA7F88AQ50002245-7E17600C-7D0A-4B8A-AB63-D2A773F98357Q55023730-3BACC42D-6D86-4404-AF78-4D214D0D8817Q55339450-A65DAD2B-8932-4206-9C65-AD7F2BC1A37BQ58552610-02183CB4-8C7B-4D70-ACC4-42BCA5B1B4C3
P2860
description
2017 nî lūn-bûn
@nan
2017年の論文
@ja
2017年論文
@yue
2017年論文
@zh-hant
2017年論文
@zh-hk
2017年論文
@zh-mo
2017年論文
@zh-tw
2017年论文
@wuu
2017年论文
@zh
2017年论文
@zh-cn
name
Nusinersen: First Global Approval.
@en
Nusinersen: First Global Approval.
@nl
type
label
Nusinersen: First Global Approval.
@en
Nusinersen: First Global Approval.
@nl
prefLabel
Nusinersen: First Global Approval.
@en
Nusinersen: First Global Approval.
@nl
P2860
P1433
P1476
Nusinersen: First Global Approval.
@en
P2093
Sheridan M Hoy
P2860
P2888
P304
P356
10.1007/S40265-017-0711-7
P577
2017-02-22T00:00:00Z