Gene transfer may be preventive but not curative for a lysosomal transport disorder.
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Is genetic rescue of cystinosis an achievable treatment goal?Quantitative in vivo and ex vivo confocal microscopy analysis of corneal cystine crystals in the Ctns knockout mouseHematopoietic stem cell gene therapy for the multisystemic lysosomal storage disorder cystinosis.The pathogenesis of cystinosis: mechanisms beyond cystine accumulation.
P2860
Gene transfer may be preventive but not curative for a lysosomal transport disorder.
description
2008 nî lūn-bûn
@nan
2008年の論文
@ja
2008年学术文章
@wuu
2008年学术文章
@zh-cn
2008年学术文章
@zh-hans
2008年学术文章
@zh-my
2008年学术文章
@zh-sg
2008年學術文章
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2008年學術文章
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2008年學術文章
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name
Gene transfer may be preventive but not curative for a lysosomal transport disorder.
@en
Gene transfer may be preventive but not curative for a lysosomal transport disorder.
@nl
type
label
Gene transfer may be preventive but not curative for a lysosomal transport disorder.
@en
Gene transfer may be preventive but not curative for a lysosomal transport disorder.
@nl
prefLabel
Gene transfer may be preventive but not curative for a lysosomal transport disorder.
@en
Gene transfer may be preventive but not curative for a lysosomal transport disorder.
@nl
P2093
P50
P356
P1433
P1476
Gene transfer may be preventive but not curative for a lysosomal transport disorder
@en
P2093
Carole Morin
Chantal Jacquet
Claire Hippert
Grégor Dubois
Olivier Disson
Reto Schwendener
Sandy Ibanes
P304
P356
10.1038/MT.2008.126
P577
2008-06-24T00:00:00Z