Systemic AAV8-Mediated Gene Therapy Drives Whole-Body Correction of Myotubular Myopathy in Dogs.
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A New AAV10-U7-Mediated Gene Therapy Prolongs Survival and Restores Function in an ALS Mouse Model.Long-term effects of systemic gene therapy in a canine model of myotubular myopathy.Systemic AAV Gene Therapy Close to Clinical Trials for Several Neuromuscular Diseases.Long-term effects of systemic gene therapy On gait in a canine model of myotubular myopathy.Linker proteins restore basement membrane and correct LAMA2-related muscular dystrophy in mice.Rescue of Pompe disease in mice by AAV-mediated liver delivery of secretable acid α-glucosidase.A multicenter, retrospective medical record review of X-linked myotubular myopathy: The recensus study.Rescue of GSDIII Phenotype with Gene Transfer Requires Liver- and Muscle-Targeted GDE Expression.Micro-dystrophin gene therapy goes systemic in Duchenne muscular dystrophy patients.Intravenous Administration of a MTMR2-Encoding AAV Vector Ameliorates the Phenotype of Myotubular Myopathy in Mice.Centronuclear myopathies under attack: A plethora of therapeutic targetsDose-Dependent Effects of FKRP Gene-Replacement Therapy on Functional Rescue and Longevity in Dystrophic MiceTamoxifen prolongs survival and alleviates symptoms in mice with fatal X-linked myotubular myopathy
P2860
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P2860
Systemic AAV8-Mediated Gene Therapy Drives Whole-Body Correction of Myotubular Myopathy in Dogs.
description
2017 nî lūn-bûn
@nan
2017年の論文
@ja
2017年論文
@yue
2017年論文
@zh-hant
2017年論文
@zh-hk
2017年論文
@zh-mo
2017年論文
@zh-tw
2017年论文
@wuu
2017年论文
@zh
2017年论文
@zh-cn
name
Systemic AAV8-Mediated Gene Th ...... f Myotubular Myopathy in Dogs.
@en
type
label
Systemic AAV8-Mediated Gene Th ...... f Myotubular Myopathy in Dogs.
@en
prefLabel
Systemic AAV8-Mediated Gene Th ...... f Myotubular Myopathy in Dogs.
@en
P2093
P2860
P50
P1433
P1476
Systemic AAV8-Mediated Gene Th ...... f Myotubular Myopathy in Dogs.
@en
P2093
Ana Buj-Bello
Annie G Brezovec
Barbara K Smith
Christine Le Bec
David L Mack
Federico Mingozzi
Jennifer L Strande
Jessica M Snyder
P2860
P304
P356
10.1016/J.YMTHE.2017.02.004
P577
2017-02-22T00:00:00Z