Development of an optimized AAV2/5 gene therapy vector for Leber congenital amaurosis owing to defects in RPE65.

Development of an optimized AAV2/5 gene therapy vector for Leber congenital amaurosis owing to defects in RPE65.

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http://www.wikidata.org/entity/Q40571621
Correction of Monogenic and Common Retinal Disorders with Gene Therapy.Inclusion of the Woodchuck Hepatitis Virus Posttranscriptional Regulatory Element Enhances AAV2-Driven Transduction of Mouse and Human RetinaLeber's Congenital Amaurosis and Gene Therapy.Leber congenital amaurosis/early-onset severe retinal dystrophy: clinical features, molecular genetics and therapeutic interventions.Concepts and Strategies in Retinal Gene Therapy.Rare Diseases: Drug Discovery and Informatics Resource.Guiding Lights in Genome Editing for Inherited Retinal Disorders: Implications for Gene and Cell Therapy.A novel adeno-associated virus capsid with enhanced neurotropism corrects a lysosomal transmembrane enzyme deficiency.A Drug-Tunable Gene Therapy for Broad-Spectrum Protection against Retinal Degeneration
P2860

Development of an optimized AAV2/5 gene therapy vector for Leber congenital amaurosis owing to defects in RPE65.

Item
http://www.wikidata.org/entity/Q40571621
description
2016 nî lūn-bûn
@nan
2016年の論文
@ja
2016年論文
@yue
2016年論文
@zh-hant
2016年論文
@zh-hk
2016年論文
@zh-mo
2016年論文
@zh-tw
2016年论文
@wuu
2016年论文
@zh
2016年论文
@zh-cn
name
Development of an optimized AA ...... sis owing to defects in RPE65.
@en
type
label
Development of an optimized AA ...... sis owing to defects in RPE65.
@en
prefLabel
Development of an optimized AA ...... sis owing to defects in RPE65.
@en
P1433
P1476
P2093
P2860
P2888
P304
P31
P356
P433
P478
P50
P577
P6179
P698
P921
P932
P356
P1433
P1476
Development of an optimized AA ...... osis owing to defects in RPE65
@en
P2093
P2860
P2888
P304
P31
P356
P433
P478
P50
P577
P6179
P698
P921
P932