Repair of CFTR mRNA by spliceosome-mediated RNA trans-splicing. - Wikidata - wikimedia - TriplyDB

Repair of CFTR mRNA by spliceosome-mediated RNA trans-splicing.

Repair of CFTR mRNA by spliceosome-mediated RNA trans-splicing.

http://www.wikidata.org/entity/Q40906944

about

mRNA trans-splicing in gene therapy for genetic diseases Chimeric RNAs in cancer and normal physiology.New high-technology products for the treatment of haemophilia.Exon exchange approach to repair Duchenne dystrophin transcripts Expression of Herpes Simplex Virus Thymidine Kinase/Ganciclovir by RNA Trans-Splicing Induces Selective Killing of HIV-Producing Cells.K14 mRNA reprogramming for dominant epidermolysis bullosa simplex.Reprogramming of tau alternative splicing by spliceosome-mediated RNA trans-splicing: implications for tauopathies.5' exon replacement and repair by spliceosome-mediated RNA trans-splicing Identification of a splicing enhancer in MLH1 using COMPARE, a new assay for determination of relative RNA splicing efficiencies Current status of gene therapy for inherited lung diseases Type XVII collagen gene mutations in junctional epidermolysis bullosa and prospects for gene therapy.Trans-splicing repair of mutant p53 suppresses the growth of hepatocellular carcinoma cells in vitro and in vivo.Targeted genetic repair: an emerging approach to genetic therapy.Messenger RNA reprogramming by spliceosome-mediated RNA trans-splicing Functional repair of p53 mutation in colorectal cancer cells using trans-splicing.Repair of rhodopsin mRNA by spliceosome-mediated RNA trans-splicing: a new approach for autosomal dominant retinitis pigmentosa.The cystic fibrosis gene: a molecular genetic perspective Modulating the expression of disease genes with RNA-based therapy.Replacement of huntingtin exon 1 by trans-splicing.Gene therapy for muscular dystrophy: current progress and future prospects.New developments in the use of gene therapy to treat Duchenne muscular dystrophy.Construction and validation of an RNA trans-splicing molecule suitable to repair a large number of COL7A1 mutations.Dysferlin rescue by spliceosome-mediated pre-mRNA trans-splicing targeting introns harbouring weakly defined 3' splice sites.Targeting Splicing in the Treatment of Human Disease Functional cystic fibrosis transmembrane conductance regulator expression in cystic fibrosis airway epithelial cells by AAV6.2-mediated segmental trans-splicing Using 5'-PTMs to repair mutant beta-globin transcripts.Adeno-Associated Virus (AAV) gene therapy for cystic fibrosis: current barriers and recent developments.Development of spliceosome-mediated RNA trans-splicing (SMaRT) for the correction of inherited skin diseases.Full-length dysferlin expression driven by engineered human dystrophic blood derived CD133+ stem cells.Optimization of trans-Splicing for Huntington's Disease RNA Therapy.Naturally occurring heterologous trans-splicing of adenovirus RNA with host cellular transcripts during infection.Correction of dystrophia myotonica type 1 pre-mRNA transcripts by artificial trans-splicing.Molecular barcoding of viral vectors enables mapping and optimization of mRNA trans-splicing.Gene Therapy via Trans-Splicing for LMNA-Related Congenital Muscular Dystrophy.Spliceosome-Mediated Pre-mRNA trans-Splicing Can Repair CEP290 mRNA.Centronuclear myopathies under attack: A plethora of therapeutic targets

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Repair of CFTR mRNA by spliceosome-mediated RNA trans-splicing.

http://www.wikidata.org/entity/Q40906944

description

2000 nî lūn-bûn

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2000年の論文

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2000年学术文章

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2000年学术文章

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2000年学术文章

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2000年学术文章

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2000年学术文章

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2000年學術文章

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2000年學術文章

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2000年學術文章

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name

Repair of CFTR mRNA by spliceosome-mediated RNA trans-splicing.

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type

label

Repair of CFTR mRNA by spliceosome-mediated RNA trans-splicing.

@en

prefLabel

Repair of CFTR mRNA by spliceosome-mediated RNA trans-splicing.

@en

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Repair of CFTR mRNA by spliceosome-mediated RNA trans-splicing.

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Cohn JA

http://www.w3.org/2001/XMLSchema#string

Garcia-Blanco MA

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Kole J

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Mansfield SG

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Mitchell LG

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Puttaraju M

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Yang CC

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P2860

Expanded sequence dependence of thermodynamic parameters improves prediction of RNA secondary structure

Identification of the cystic fibrosis gene: cloning and characterization of complementary DNA

Human acyl-CoA:cholesterol acyltransferase-1 (ACAT-1) gene organization and evidence that the 4.3-kilobase ACAT-1 mRNA is produced from two different chromosomes

Correction of the ion transport defect in cystic fibrosis transgenic mice by gene therapy

Natural trans-splicing in carnitine octanoyltransferase pre-mRNAs in rat liver

Gene repair using chimeric RNA/DNA oligonucleotides.

A spliced leader is present on a subset of mRNAs from the human parasite Schistosoma mansoni.

Airway epithelial CFTR mRNA expression in cystic fibrosis patients after repetitive administration of a recombinant adenovirus.

RNA molecules containing exons originating from different members of the cytochrome P450 2C gene subfamily (CYP2C) in human epidermis and liver

In vivo retroviral gene transfer into human bronchial epithelia of xenografts.

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10.1038/SJ.GT.3301307

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22

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