In vivo gene therapy of hemophilia B: sustained partial correction in factor IX-deficient dogs.
about
Persistent expression of human clotting factor IX from mouse liver after intravenous injection of adeno-associated virus vectorsIntravenous injection of a foamy virus vector to correct canine SCID-X1.Strategy of liver-directed gene therapy: present status and future prospects.Gene therapy for the hemophilias.Reactivation of the previously silenced cytomegalovirus major immediate-early promoter in the mouse liver: involvement of NFkappaB.The resistance of retroviral vectors produced from human cells to serum inactivation in vivo and in vitro is primate species dependent.Efficient gene transfer into human hepatocytes by baculovirus vectorsGene therapy for hemophilia.Transient disruption of intercellular junctions enables baculovirus entry into nondividing hepatocytes.Factor IX ectopically expressed in platelets can be stored in alpha-granules and corrects the phenotype of hemophilia B mice.Gene therapy: a 2001 perspective.Adenovirus-mediated urokinase gene transfer induces liver regeneration and allows for efficient retrovirus transduction of hepatocytes in vivo.Myoblast transfer of human erythropoietin gene in a mouse model of renal failureAdenoviral-mediated gene transfer to fetal pulmonary epithelia in vitro and in vivo.Haemophilias: advances towards genetic engineering replacement therapy.Gene therapy: here to stay.Hyperactive sleeping beauty transposase enables persistent phenotypic correction in mice and a canine model for hemophilia B.Platelets as delivery systems for disease treatmentsGene therapy for haemophilia.The role of progenitor cells in repair of liver injury and in liver transplantation.Parvovirus-mediated gene transfer for the haemophilias.Efficacy and safety of long-term prophylaxis in severe hemophilia A dogs following liver gene therapy using AAV vectors.Protein replacement therapy and gene transfer in canine models of hemophilia A, hemophilia B, von willebrand disease, and factor VII deficiency.In vivo hepatic gene therapy: complete albeit transient correction of factor IX deficiency in hemophilia B dogs.Theodore E. Woodward Award. AAV-mediated gene transfer for hemophilia.Long-term expression of human coagulation factor VIII and correction of hemophilia A after in vivo retroviral gene transfer in factor VIII-deficient mice.A general method for the generation of high-titer, pantropic retroviral vectors: highly efficient infection of primary hepatocytes.Pseudotransduction of hepatocytes by using concentrated pseudotyped vesicular stomatitis virus G glycoprotein (VSV-G)-Moloney murine leukemia virus-derived retrovirus vectors: comparison of VSV-G and amphotropic vectors for hepatic gene transfer.Stable delivery of physiologic levels of recombinant erythropoietin to the systemic circulation by intramuscular injection of replication-defective adenovirus.Understanding hereditary diseases using the dog and human as companion model systems.Engineering lymphocyte subsets: tools, trials and tribulationsStable gene transfer and expression of human blood coagulation factor IX after intramuscular injection of recombinant adeno-associated virus.The effects of PVP(Fe(III)) catalyst on polymer molecular weight and gene delivery via biodegradable cross-linked polyethylenimine.Treatment of Hemophilia A in Utero and Postnatally using Sheep as a Model for Cell and Gene DeliveryA factor IX-deficient mouse model for hemophilia B gene therapy.Hepatic gene therapy: efficient gene delivery and expression in primary hepatocytes utilizing a conjugated adenovirus-DNA complex.Gene therapy for inborn errors of liver metabolism: progress towards clinical applicationsIn vivo models of haemophilia - status on current knowledge of clinical phenotypes and therapeutic interventions.Supramolecular nanosubstrate-mediated delivery for reprogramming and transdifferentiation of mammalian cells.Semi-automated closed system manufacturing of lentivirus gene-modified haematopoietic stem cells for gene therapy
P2860
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P2860
In vivo gene therapy of hemophilia B: sustained partial correction in factor IX-deficient dogs.
description
1993 nî lūn-bûn
@nan
1993年の論文
@ja
1993年論文
@yue
1993年論文
@zh-hant
1993年論文
@zh-hk
1993年論文
@zh-mo
1993年論文
@zh-tw
1993年论文
@wuu
1993年论文
@zh
1993年论文
@zh-cn
name
In vivo gene therapy of hemoph ...... n in factor IX-deficient dogs.
@en
type
label
In vivo gene therapy of hemoph ...... n in factor IX-deficient dogs.
@en
prefLabel
In vivo gene therapy of hemoph ...... n in factor IX-deficient dogs.
@en
P2093
P921
P356
P1433
P1476
In vivo gene therapy of hemoph ...... n in factor IX-deficient dogs.
@en
P2093
Bellinger DA
Brinkhous KM
Finegold M
Rothenberg S
Thompson AR
P304
P356
10.1126/SCIENCE.8211118
P407
P577
1993-10-01T00:00:00Z