Four-year prospective clinical trial of agalsidase alfa in children with Fabry disease.
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Agalsidase alfa: a review of its use in the management of Fabry diseaseEfficacy and safety of enzyme-replacement-therapy with agalsidase alfa in 36 treatment-naïve Fabry disease patients.Agalsidase alfa in pediatric patients with Fabry disease: a 6.5-year open-label follow-up study.Enzyme replacement therapy for Fabry disease: some answers but more questionsUpdate on role of agalsidase alfa in management of Fabry disease.Carboxyl-terminal truncations alter the activity of the human α-galactosidase ARecommendations for initiation and cessation of enzyme replacement therapy in patients with Fabry disease: the European Fabry Working Group consensus document.Evaluation of the efficacy and safety of three dosing regimens of agalsidase alfa enzyme replacement therapy in adults with Fabry disease.Agalsidase benefits renal histology in young patients with Fabry disease.An open-label clinical trial of agalsidase alfa enzyme replacement therapy in children with Fabry disease who are naïve to enzyme replacement therapy.Reduction of Plasma Globotriaosylsphingosine Levels After Switching from Agalsidase Alfa to Agalsidase Beta as Enzyme Replacement Therapy for Fabry DiseasePain in Fabry Disease: Practical Recommendations for Diagnosis and Treatment.Fabry disease: clinical and genotypic aspects of three cases in first degree relatives.Fabry disease: a review of current management strategies.Effects of enzyme replacement therapy in Fabry disease--a comprehensive review of the medical literature.Safety of agalsidase alfa in patients with Fabry disease under 7 years.Enzyme replacement in neuronal storage disorders in the pediatric population.Fabry disease in children: agalsidase-beta enzyme replacement therapy.Long-term effectiveness of enzyme replacement therapy in Fabry disease: results from the NCS-LSD cohort study.Therapeutic goals in the treatment of Fabry disease.Agalsidase treatment for Fabry disease: uses and rivalries.Fabry disease
P2860
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P2860
Four-year prospective clinical trial of agalsidase alfa in children with Fabry disease.
description
2010 nî lūn-bûn
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2010年の論文
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2010年学术文章
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2010年学术文章
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2010年学术文章
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2010年学术文章
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2010年学术文章
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2010年學術文章
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name
Four-year prospective clinical trial of agalsidase alfa in children with Fabry disease.
@en
Four-year prospective clinical trial of agalsidase alfa in children with Fabry disease.
@nl
type
label
Four-year prospective clinical trial of agalsidase alfa in children with Fabry disease.
@en
Four-year prospective clinical trial of agalsidase alfa in children with Fabry disease.
@nl
prefLabel
Four-year prospective clinical trial of agalsidase alfa in children with Fabry disease.
@en
Four-year prospective clinical trial of agalsidase alfa in children with Fabry disease.
@nl
P2093
P1476
Four-year prospective clinical trial of agalsidase alfa in children with Fabry disease.
@en
P2093
Christoph Kampmann
Gregory M Pastores
Joe T R Clarke
Karen Johnson
Raphael Schiffmann
Rick A Martin
Tyler Reimschisel
Victoria Castaneda
Y Howard Lien
P304
832-7, 837.e1
P356
10.1016/J.JPEDS.2009.11.007
P407
P50
P577
2010-01-25T00:00:00Z