Restoration of human dystrophin following transplantation of exon-skipping-engineered DMD patient stem cells into dystrophic mice.
about
Enhanced exon-skipping induced by U7 snRNA carrying a splicing silencer sequence: Promising tool for DMD therapyThe emerging role of viral vectors as vehicles for DMD gene editingPotential of adipose-derived stem cells in muscular regenerative therapiesAdvancements in stem cells treatment of skeletal muscle wastingPerspectives of stem cell therapy in Duchenne muscular dystrophyCurrent understanding of molecular pathology and treatment of cardiomyopathy in duchenne muscular dystrophyRepairing skeletal muscle: regenerative potential of skeletal muscle stem cells.Human skeletal muscle-derived CD133(+) cells form functional satellite cells after intramuscular transplantation in immunodeficient host miceA home away from home: challenges and opportunities in engineering in vitro muscle satellite cell nichesExon exchange approach to repair Duchenne dystrophin transcriptsDystrophic Cardiomyopathy-Potential Role of Calcium in Pathogenesis, Treatment and Novel TherapiesHuman skeletal muscle xenograft as a new preclinical model for muscle disordersLentiviral vectors can be used for full-length dystrophin gene therapyChronic binge alcohol consumption alters myogenic gene expression and reduces in vitro myogenic differentiation potential of myoblasts from rhesus macaquesInfluence of immune responses in gene/stem cell therapies for muscular dystrophies.Satellite cells and the muscle stem cell nicheGene and cell-mediated therapies for muscular dystrophy.Contribution of human muscle-derived cells to skeletal muscle regeneration in dystrophic host mice.Evaluation of Muscle Performance in Mice by Treadmill Exhaustion Test and Whole-limb Grip Strength Assay.Gene therapy for muscular dystrophies: progress and challengesExon-skipping strategy by ratio modulation between cytoprotective versus pro-apoptotic clusterin forms increased sensitivity of LNCaP to cell death.Progress in muscular dystrophy research with special emphasis on gene therapy.Coaxing stem cells for skeletal muscle repairTherapeutic approaches to muscular dystrophy.Current status of pharmaceutical and genetic therapeutic approaches to treat DMD.Stem cell transplantation for treating Duchenne muscular dystrophy: A Web of Science-based literature analysisSculpting chromatin beyond the double helix: epigenetic control of skeletal myogenesis.Systemic delivery of allogenic muscle stem cells induces long-term muscle repair and clinical efficacy in duchenne muscular dystrophy dogsThe effect of the muscle environment on the regenerative capacity of human skeletal muscle stem cells.Cell therapy in muscular dystrophies: many promises in mice and dogs, few facts in patients.Autologous skeletal muscle derived cells expressing a novel functional dystrophin provide a potential therapy for Duchenne Muscular Dystrophy.The emerging biology of muscle stem cells: implications for cell-based therapies.Intrinsic ability of adult stem cell in skeletal muscle: an effective and replenishable resource to the establishment of pluripotent stem cellsImpaired regeneration: A role for the muscle microenvironment in cancer cachexia.Engineering skeletal muscle repair.Peptide-mediated cellular delivery of oligonucleotide-based therapeutics in vitro: quantitative evaluation of overall efficacy employing easy to handle reporter systems.miRNAS in normal and diseased skeletal muscle.Skeletal muscle as a paradigm for regenerative biology and medicine.Gene therapy for muscular dystrophy: current progress and future prospects.Cell based therapy for Duchenne muscular dystrophy.
P2860
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P2860
Restoration of human dystrophin following transplantation of exon-skipping-engineered DMD patient stem cells into dystrophic mice.
description
2007 nî lūn-bûn
@nan
2007年の論文
@ja
2007年学术文章
@wuu
2007年学术文章
@zh-cn
2007年学术文章
@zh-hans
2007年学术文章
@zh-my
2007年学术文章
@zh-sg
2007年學術文章
@yue
2007年學術文章
@zh
2007年學術文章
@zh-hant
name
Restoration of human dystrophi ...... em cells into dystrophic mice.
@en
Restoration of human dystrophi ...... em cells into dystrophic mice.
@nl
type
label
Restoration of human dystrophi ...... em cells into dystrophic mice.
@en
Restoration of human dystrophi ...... em cells into dystrophic mice.
@nl
prefLabel
Restoration of human dystrophi ...... em cells into dystrophic mice.
@en
Restoration of human dystrophi ...... em cells into dystrophic mice.
@nl
P2093
P50
P1433
P1476
Restoration of human dystrophi ...... em cells into dystrophic mice.
@en
P2093
Andrea Farini
Aurélie Goyenvalle
Luis Garcia
Marzia Belicchi
Maurizio Battistelli
Rachid Benchaouir
Roberto Bottinelli
P304
P356
10.1016/J.STEM.2007.09.016
P407
P577
2007-12-01T00:00:00Z