Long-term normalization in the central nervous system, ocular manifestations, and skeletal deformities by a single systemic adenovirus injection into neonatal mice with mucopolysaccharidosis VII.
about
Gene therapy for mucopolysaccharidosisThe effect of neonatal gene therapy on skeletal manifestations in mucopolysaccharidosis VII dogs after a decade.Recent advances in the pharmacology of neurological gene therapy.Overcoming the blood-brain barrier with high-dose enzyme replacement therapy in murine mucopolysaccharidosis VII.Perinatal gene transfer to the liver.Gene therapy approaches for lysosomal storage disease: next-generation treatment.Neonatal cellular and gene therapies for mucopolysaccharidoses: the earlier the better?Current therapies for Morquio A syndrome and their clinical outcomes.Gene therapy for the neurological manifestations in lysosomal storage disorders.Recent advances in gene therapy for lysosomal storage disorders.Gene therapy for Mucopolysaccharidoses.
P2860
Q24631135-DE9B7536-9B0A-4755-BC77-B34CB2E77368Q30540876-EE360807-7680-427F-81F1-0E814F9C98C1Q33985688-96CD9321-6586-472C-BCA7-144A70D87334Q34078512-1E975594-CD4C-4E78-AECC-3EF63C3C0FC2Q35238390-C13B076C-C01D-40AA-98F3-2ED04DEA68F4Q36147475-1A2494B1-DE64-4B3F-BA50-A51B834AD73AQ36582259-65FF9493-CB97-4147-8383-0D380369A012Q37646091-9943FA67-C9B7-4BB2-90EF-B1560D5A82F7Q38200599-5A84A395-F872-4689-A54B-7830B644D27CQ38546492-466CE03B-5FB1-473A-A148-4A6C45BFEF91Q47558790-61FCD905-0EAE-4F57-BC5C-2ED0E493178D
P2860
Long-term normalization in the central nervous system, ocular manifestations, and skeletal deformities by a single systemic adenovirus injection into neonatal mice with mucopolysaccharidosis VII.
description
2003 nî lūn-bûn
@nan
2003年の論文
@ja
2003年学术文章
@wuu
2003年学术文章
@zh
2003年学术文章
@zh-cn
2003年学术文章
@zh-hans
2003年学术文章
@zh-my
2003年学术文章
@zh-sg
2003年學術文章
@yue
2003年學術文章
@zh-hant
name
Long-term normalization in the ...... ith mucopolysaccharidosis VII.
@en
Long-term normalization in the ...... ith mucopolysaccharidosis VII.
@nl
type
label
Long-term normalization in the ...... ith mucopolysaccharidosis VII.
@en
Long-term normalization in the ...... ith mucopolysaccharidosis VII.
@nl
prefLabel
Long-term normalization in the ...... ith mucopolysaccharidosis VII.
@en
Long-term normalization in the ...... ith mucopolysaccharidosis VII.
@nl
P2093
P2860
P356
P1433
P1476
Long-term normalization in the ...... ith mucopolysaccharidosis VII.
@en
P2093
Fukuhara Y
P2860
P2888
P304
P356
10.1038/SJ.GT.3301869
P577
2003-03-01T00:00:00Z