Enzyme-replacement therapy with agalsidase alfa in children with Fabry disease.
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Enzyme replacement therapy for Anderson-Fabry diseaseEnzyme replacement therapy for Anderson-Fabry diseaseSafety and efficacy of enzyme replacement therapy in the nephropathy of Fabry diseaseEnzyme replacement therapy for Anderson-Fabry diseasePain management strategies for neuropathic pain in Fabry disease--a systematic reviewAgalsidase alfa: a review of its use in the management of Fabry diseaseNeuropathic and cerebrovascular correlates of hearing loss in Fabry diseaseAutonomic neuropathy in Fabry disease: a prospective study using the Autonomic Symptom Profile and cardiovascular autonomic function testsStroke and Fabry disease.Enzyme replacement therapy and beyond-in memoriam Roscoe O. Brady, M.D. (1923-2016).Update on role of agalsidase alfa in management of Fabry disease.Recommendations for initiation and cessation of enzyme replacement therapy in patients with Fabry disease: the European Fabry Working Group consensus document.Proteomics of specific treatment-related alterations in Fabry disease: a strategy to identify biological abnormalities.Rapid Immunochromatographic Detection of Serum Anti-α-Galactosidase A Antibodies in Fabry Patients after Enzyme Replacement Therapy.Enzyme replacement therapy for Anderson-Fabry disease: A complementary overview of a Cochrane publication through a linear regression and a pooled analysis of proportions from cohort studies.Effect of reduced agalsidase Beta dosage in fabry patients: the Australian experienceAgalsidase benefits renal histology in young patients with Fabry disease.Novel therapeutic targets for the treatment of Fabry disease.Short-term efficacy of enzyme replacement therapy in Korean patients with Fabry disease.An open-label clinical trial of agalsidase alfa enzyme replacement therapy in children with Fabry disease who are naïve to enzyme replacement therapy.Globotriaosylceramide induces oxidative stress and up-regulates cell adhesion molecule expression in Fabry disease endothelial cells.Assessment of renal pathology and dysfunction in children with Fabry disease.Fabry disease during childhood: clinical manifestations and treatment with agalsidase alfa.Early therapeutic intervention in females with Fabry disease?Early cardiac changes in children with anderson-fabry disease.Renal complications of Fabry disease in childrenAgalsidase alfa (Replagal) in the treatment of Anderson-Fabry diseaseFabry disease in children and the effects of enzyme replacement treatment.Gender Differences in the Application of Spanish Criteria for Initiation of Enzyme Replacement Therapy for Fabry Disease in the Fabry Outcome Survey.Fabry disease: a review of current management strategies.Effects of enzyme replacement therapy in Fabry disease--a comprehensive review of the medical literature.Safety of agalsidase alfa in patients with Fabry disease under 7 years.Fabry disease, enzyme replacement therapy and the significance of antibody responses.Neurological features of Fabry disease: clinical, pathophysiological aspects and therapy.Natural course of Fabry disease and the effectiveness of enzyme replacement therapy: a systematic review and meta-analysis: effectiveness of ERT in different disease stages.Fabry disease in infancy and early childhood: a systematic literature review.Perspectives in Pediatric Pathology, Chapter 21. Testicular Pathology in Heritable Metabolic Disease.Fabry's disease: an example of cardiorenal syndrome type 5.Neuro-Otological and Peripheral Nerve Involvement in Fabry Disease.Urine bikunin as a marker of renal impairment in Fabry's disease.
P2860
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P2860
Enzyme-replacement therapy with agalsidase alfa in children with Fabry disease.
description
2006 nî lūn-bûn
@nan
2006年の論文
@ja
2006年学术文章
@wuu
2006年学术文章
@zh
2006年学术文章
@zh-cn
2006年学术文章
@zh-hans
2006年学术文章
@zh-my
2006年学术文章
@zh-sg
2006年學術文章
@yue
2006年學術文章
@zh-hant
name
Enzyme-replacement therapy with agalsidase alfa in children with Fabry disease.
@en
Enzyme-replacement therapy with agalsidase alfa in children with Fabry disease.
@nl
type
label
Enzyme-replacement therapy with agalsidase alfa in children with Fabry disease.
@en
Enzyme-replacement therapy with agalsidase alfa in children with Fabry disease.
@nl
prefLabel
Enzyme-replacement therapy with agalsidase alfa in children with Fabry disease.
@en
Enzyme-replacement therapy with agalsidase alfa in children with Fabry disease.
@nl
P2093
P356
P1433
P1476
Enzyme-replacement therapy with agalsidase alfa in children with Fabry disease.
@en
P2093
Catharina Whybra
Chevalia Robinson
Christoph Kampmann
Gregory Pastores
Joe T R Clarke
Margaret Timmons
Michael Beck
Raphael Schiffmann
Roscoe O Brady
Y Howard Lien
P304
P356
10.1542/PEDS.2005-2895
P407
P577
2006-09-01T00:00:00Z