Neurocognitive and somatic stabilization in pediatric patients with severe Mucopolysaccharidosis Type I after 52 weeks of intravenous brain-penetrating insulin receptor antibody-iduronidase fusion protein (valanafusp alpha): an open label phase 1-2 t
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Neurocognitive and somatic stabilization in pediatric patients with severe Mucopolysaccharidosis Type I after 52 weeks of intravenous brain-penetrating insulin receptor antibody-iduronidase fusion protein (valanafusp alpha): an open label phase 1-2 t
description
wetenschappelijk artikel
@nl
наукова стаття, опублікована в липні 2018
@uk
name
Neurocognitive and somatic sta ...... ha): an open label phase 1-2 t
@en
Neurocognitive and somatic sta ...... ody-iduronidase fusion protein
@nl
type
label
Neurocognitive and somatic sta ...... ha): an open label phase 1-2 t
@en
Neurocognitive and somatic sta ...... ody-iduronidase fusion protein
@nl
prefLabel
Neurocognitive and somatic sta ...... ha): an open label phase 1-2 t
@en
Neurocognitive and somatic sta ...... ody-iduronidase fusion protein
@nl
P2093
P2860
P50
P1476
Neurocognitive and somatic sta ...... ha): an open label phase 1-2 t
@en
P2093
Amauri Dalla Corte
Carol Nguyen
Igor Nestrasil
Karina Carvalho Donis
Luciana Giugliani
Mathias Schmidt
Roberto Giugliani
Steven Chen
P2860
P2888
P356
10.1186/S13023-018-0849-8
P407
P577
2018-07-05T00:00:00Z
P6179
1105313991