about
Identification of age-dependent motor and neuropsychological behavioural abnormalities in a mouse model of Mucopolysaccharidosis Type IIMacrophage enzyme and reduced inflammation drive brain correction of mucopolysaccharidosis IIIB by stem cell gene therapy.Understanding deregulated cellular and molecular dynamics in the haematopoietic stem cell niche to develop novel therapeutics for bone marrow fibrosis.A novel adeno-associated virus capsid with enhanced neurotropism corrects a lysosomal transmembrane enzyme deficiency.Brain-targeted stem cell gene therapy corrects mucopolysaccharidosis type II via multiple mechanisms.An Improved Adeno-Associated Virus Vector for Neurological Correction of the Mouse Model of Mucopolysaccharidosis IIIA
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description
researcher ORCID ID = 0000-0001-6138-8916
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wetenschapper
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name
Hélène Gleitz
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Hélène Gleitz
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Hélène Gleitz
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type
label
Hélène Gleitz
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Hélène Gleitz
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Hélène Gleitz
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prefLabel
Hélène Gleitz
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Hélène Gleitz
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Hélène Gleitz
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0000-0001-6138-8916