about
Rescue of Pompe disease in mice by AAV-mediated liver delivery of secretable acid α-glucosidase.Late-onset Pompe disease in France: molecular features and epidemiology from a nationwide studyLong-term benefit of enzyme replacement therapy with alglucosidase alfa in adults with Pompe disease: prospective analysis from the French Pompe Registry
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description
researcher
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wetenschapper
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name
Pascal Laforet
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Pascal Laforet
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type
label
Pascal Laforet
@en
Pascal Laforet
@nl
prefLabel
Pascal Laforet
@en
Pascal Laforet
@nl
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0000-0002-4489-4718