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Q24595945-54893FC4-81C0-4EFF-AB1B-2E64308311BF
Q24595945-54893FC4-81C0-4EFF-AB1B-2E64308311BF
BestRank
Statement
http://www.wikidata.org/entity/statement/Q24595945-54893FC4-81C0-4EFF-AB1B-2E64308311BF
Update on treatment of lysosomal storage diseases
P2860
Q24595945-54893FC4-81C0-4EFF-AB1B-2E64308311BF
BestRank
Statement
http://www.wikidata.org/entity/statement/Q24595945-54893FC4-81C0-4EFF-AB1B-2E64308311BF
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Statement
wasDerivedFrom
d249c444883b4b5e01de61a4ac13403aba0a271c
P2860
The role of the iminosugar N-butyldeoxynojirimycin (miglustat) in the management of type I (non-neuronopathic) Gaucher disease: a position statement