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Q31132177-2DEAA7DF-E6CE-47C0-91E6-6C72051EB350
Q31132177-2DEAA7DF-E6CE-47C0-91E6-6C72051EB350
BestRank
Statement
http://www.wikidata.org/entity/statement/Q31132177-2DEAA7DF-E6CE-47C0-91E6-6C72051EB350
Myosin7a deficiency results in reduced retinal activity which is improved by gene therapy.
P2860
Q31132177-2DEAA7DF-E6CE-47C0-91E6-6C72051EB350
BestRank
Statement
http://www.wikidata.org/entity/statement/Q31132177-2DEAA7DF-E6CE-47C0-91E6-6C72051EB350
rank
NormalRank
type
BestRank
Statement
wasDerivedFrom
787e8f3cb978c2cc3e0bdf8d252fe83a7ac245cc
P2860
Leber congenital amaurosis due to RPE65 mutations and its treatment with gene therapy