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Q31132177-940C873F-B90C-4195-9FFE-BD3AB71DFEA4
Q31132177-940C873F-B90C-4195-9FFE-BD3AB71DFEA4
BestRank
Statement
http://www.wikidata.org/entity/statement/Q31132177-940C873F-B90C-4195-9FFE-BD3AB71DFEA4
Myosin7a deficiency results in reduced retinal activity which is improved by gene therapy.
P2860
Q31132177-940C873F-B90C-4195-9FFE-BD3AB71DFEA4
BestRank
Statement
http://www.wikidata.org/entity/statement/Q31132177-940C873F-B90C-4195-9FFE-BD3AB71DFEA4
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wasDerivedFrom
787e8f3cb978c2cc3e0bdf8d252fe83a7ac245cc
P2860
Retinal gene therapy with a large MYO7A cDNA using adeno-associated virus.