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Q31132177-9DDF850F-A4AF-4228-92A1-81C1273B577E
Q31132177-9DDF850F-A4AF-4228-92A1-81C1273B577E
BestRank
Statement
http://www.wikidata.org/entity/statement/Q31132177-9DDF850F-A4AF-4228-92A1-81C1273B577E
Myosin7a deficiency results in reduced retinal activity which is improved by gene therapy.
P2860
Q31132177-9DDF850F-A4AF-4228-92A1-81C1273B577E
BestRank
Statement
http://www.wikidata.org/entity/statement/Q31132177-9DDF850F-A4AF-4228-92A1-81C1273B577E
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wasDerivedFrom
787e8f3cb978c2cc3e0bdf8d252fe83a7ac245cc
P2860
Homologous recombination mediates functional recovery of dysferlin deficiency following AAV5 gene transfer