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Q33625875-849FF1FC-88FC-49D1-9F29-A2BAE13FF8CB
Q33625875-849FF1FC-88FC-49D1-9F29-A2BAE13FF8CB
BestRank
Statement
http://www.wikidata.org/entity/statement/Q33625875-849FF1FC-88FC-49D1-9F29-A2BAE13FF8CB
Delivery is key: lessons learnt from developing splice-switching antisense therapies
P2860
Q33625875-849FF1FC-88FC-49D1-9F29-A2BAE13FF8CB
BestRank
Statement
http://www.wikidata.org/entity/statement/Q33625875-849FF1FC-88FC-49D1-9F29-A2BAE13FF8CB
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e2fac1a1446f178fc13c405185d3fd4410ce3c0e
P2860
Treatment of infantile-onset spinal muscular atrophy with nusinersen: a phase 2, open-label, dose-escalation study.