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Q33678893-D9E4558B-4F8C-4CCD-867B-8822121E7FDC
Q33678893-D9E4558B-4F8C-4CCD-867B-8822121E7FDC
BestRank
Statement
http://www.wikidata.org/entity/statement/Q33678893-D9E4558B-4F8C-4CCD-867B-8822121E7FDC
Therapy of Genetic Disorders-Novel Therapies for Duchenne Muscular Dystrophy.
P2860
Q33678893-D9E4558B-4F8C-4CCD-867B-8822121E7FDC
BestRank
Statement
http://www.wikidata.org/entity/statement/Q33678893-D9E4558B-4F8C-4CCD-867B-8822121E7FDC
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Statement
wasDerivedFrom
61b7c484cf3df392aac084b519fbf3d6f48b7719
P2860
Rescue of severely affected dystrophin/utrophin-deficient mice through scAAV-U7snRNA-mediated exon skipping