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Q33926944-9F6419F5-D9F8-413F-BBF0-1D1F5FD831F2
Q33926944-9F6419F5-D9F8-413F-BBF0-1D1F5FD831F2
BestRank
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http://www.wikidata.org/entity/statement/Q33926944-9F6419F5-D9F8-413F-BBF0-1D1F5FD831F2
Gene therapy prolongs survival and restores function in murine and canine models of myotubular myopathy.
P2860
Q33926944-9F6419F5-D9F8-413F-BBF0-1D1F5FD831F2
BestRank
Statement
http://www.wikidata.org/entity/statement/Q33926944-9F6419F5-D9F8-413F-BBF0-1D1F5FD831F2
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wasDerivedFrom
f1fbdcb5b1307576bbfb1d2b2fdcdeec3a23e4d0
P2860
AAV genome loss from dystrophic mouse muscles during AAV-U7 snRNA-mediated exon-skipping therapy.