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Q34321271-4A6BC8BB-3713-4323-9548-A47CD8AE9B27
Q34321271-4A6BC8BB-3713-4323-9548-A47CD8AE9B27
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http://www.wikidata.org/entity/statement/Q34321271-4A6BC8BB-3713-4323-9548-A47CD8AE9B27
Intramuscular scAAV9-SMN injection mediates widespread gene delivery to the spinal cord and decreases disease severity in SMA mice.
P2860
Q34321271-4A6BC8BB-3713-4323-9548-A47CD8AE9B27
BestRank
Statement
http://www.wikidata.org/entity/statement/Q34321271-4A6BC8BB-3713-4323-9548-A47CD8AE9B27
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4c7f253a35b85ad3da8a5b29ba836268bd12a181
P2860
Skeletal muscle in motor neuron diseases: therapeutic target and delivery route for potential treatments.