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Q34512451-0EB0EFFB-C64A-4C6A-BF4E-0E2A8FBAEFF8
Q34512451-0EB0EFFB-C64A-4C6A-BF4E-0E2A8FBAEFF8
BestRank
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http://www.wikidata.org/entity/statement/Q34512451-0EB0EFFB-C64A-4C6A-BF4E-0E2A8FBAEFF8
Discovery of a biomarker and lead small molecules to target r(GGGGCC)-associated defects in c9FTD/ALS.
P2860
Q34512451-0EB0EFFB-C64A-4C6A-BF4E-0E2A8FBAEFF8
BestRank
Statement
http://www.wikidata.org/entity/statement/Q34512451-0EB0EFFB-C64A-4C6A-BF4E-0E2A8FBAEFF8
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wasDerivedFrom
e7cff2f9355dc40d77e6dac66d580b1b5c13c90c
P2860
RNA toxicity from the ALS/FTD C9ORF72 expansion is mitigated by antisense intervention