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Q34545883-5DE8D24B-26FF-44BC-9FE1-219EC6CC82CF
Q34545883-5DE8D24B-26FF-44BC-9FE1-219EC6CC82CF
BestRank
Statement
http://www.wikidata.org/entity/statement/Q34545883-5DE8D24B-26FF-44BC-9FE1-219EC6CC82CF
Therapies of mucopolysaccharidosis IVA (Morquio A syndrome).
P2860
Q34545883-5DE8D24B-26FF-44BC-9FE1-219EC6CC82CF
BestRank
Statement
http://www.wikidata.org/entity/statement/Q34545883-5DE8D24B-26FF-44BC-9FE1-219EC6CC82CF
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wasDerivedFrom
08b3922368acf8d990ce73cfc18be199e9425304
P2860
Sialic acid deposition impairs the utility of AAV9, but not peptide-modified AAVs for brain gene therapy in a mouse model of lysosomal storage disease