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Q34553589-EB7F85DD-73F4-4D71-9F1F-A96ECC7C937D
Q34553589-EB7F85DD-73F4-4D71-9F1F-A96ECC7C937D
BestRank
Statement
http://www.wikidata.org/entity/statement/Q34553589-EB7F85DD-73F4-4D71-9F1F-A96ECC7C937D
Enzyme replacement therapy and beyond-in memoriam Roscoe O. Brady, M.D. (1923-2016).
P2860
Q34553589-EB7F85DD-73F4-4D71-9F1F-A96ECC7C937D
BestRank
Statement
http://www.wikidata.org/entity/statement/Q34553589-EB7F85DD-73F4-4D71-9F1F-A96ECC7C937D
rank
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type
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Statement
wasDerivedFrom
dc9b7417a335a1f78f4b1c339f1eb58217d92ba3
P2860
The pharmacological chaperone AT2220 increases recombinant human acid α-glucosidase uptake and glycogen reduction in a mouse model of Pompe disease.