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Q34561960-194957FE-7EC0-4661-B649-AF36B3AF761F
Q34561960-194957FE-7EC0-4661-B649-AF36B3AF761F
BestRank
Statement
http://www.wikidata.org/entity/statement/Q34561960-194957FE-7EC0-4661-B649-AF36B3AF761F
Ataluren treatment of patients with nonsense mutation dystrophinopathy.
P2860
Q34561960-194957FE-7EC0-4661-B649-AF36B3AF761F
BestRank
Statement
http://www.wikidata.org/entity/statement/Q34561960-194957FE-7EC0-4661-B649-AF36B3AF761F
rank
NormalRank
type
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Statement
wasDerivedFrom
864a9385ec815bb677608901419326e2379a2482
P2860
Phase 2a study of ataluren-mediated dystrophin production in patients with nonsense mutation Duchenne muscular dystrophy.