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Q35007910-0658607C-588F-49AB-8D61-394C9E18EC70
Q35007910-0658607C-588F-49AB-8D61-394C9E18EC70
BestRank
Statement
http://www.wikidata.org/entity/statement/Q35007910-0658607C-588F-49AB-8D61-394C9E18EC70
Identification and characterization of pharmacological chaperones to correct enzyme deficiencies in lysosomal storage disorders.
P2860
Q35007910-0658607C-588F-49AB-8D61-394C9E18EC70
BestRank
Statement
http://www.wikidata.org/entity/statement/Q35007910-0658607C-588F-49AB-8D61-394C9E18EC70
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fe644893afa5fd29405a99688e4105b4e2799f6c
P2860
Miglustat in adult and juvenile patients with Niemann-Pick disease type C: long-term data from a clinical trial.