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Q35034401-1A0CF4B3-F264-4AC0-9FAA-9CD8300AC6E7
Q35034401-1A0CF4B3-F264-4AC0-9FAA-9CD8300AC6E7
BestRank
Statement
http://www.wikidata.org/entity/statement/Q35034401-1A0CF4B3-F264-4AC0-9FAA-9CD8300AC6E7
Lysosomal storage disease: gene therapy on both sides of the blood-brain barrier.
P2860
Q35034401-1A0CF4B3-F264-4AC0-9FAA-9CD8300AC6E7
BestRank
Statement
http://www.wikidata.org/entity/statement/Q35034401-1A0CF4B3-F264-4AC0-9FAA-9CD8300AC6E7
rank
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type
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wasDerivedFrom
a78e705d4fa185ba7b75cd900a45acf3a89043bd
P2860
Gene therapy for lysosomal storage diseases (LSDs) in large animal models.